Parkinson's Disease Phenotypes in Patient Neuronal Cultures and Brain Organoids Improved by 2-Hydroxypropyl-β-Cyclodextrin Treatment
2-羟丙基-β-环糊精治疗可改善帕金森病患者神经元培养物和脑类器官中的帕金森病表型
期刊:Mov Disord
影响因子:7.400
doi:10.1002/mds.28810
Javier Jarazo ,Kyriaki Barmpa ,Jennifer Modamio ,Cláudia Saraiva ,Sònia Sabaté-Soler ,Isabel Rosety ,Anne Griesbeck ,Florian Skwirblies ,Gaia Zaffaroni ,Lisa M Smits ,Jihui Su ,Jonathan Arias-Fuenzalida ,Jonas Walter ,Gemma Gomez-Giro ,Anna S Monzel ,Xiaobing Qing ,Armelle Vitali ,Gerald Cruciani ,Ibrahim Boussaad ,Francesco Brunelli ,Christian Jäger ,Aleksandar Rakovic ,Wen Li ,Lin Yuan ,Emanuel Berger ,Giuseppe Arena ,Silvia Bolognin ,Ronny Schmidt ,Christoph Schröder ,Paul M A Antony ,Christine Klein ,Rejko Krüger ,Philip Seibler ,Jens C Schwamborn