Toward genome editing in X-linked RP-development of a mouse model with specific treatment relevant features
针对X连锁视网膜色素变性的基因组编辑——构建具有特定治疗相关特征的小鼠模型
期刊:Transl Res
影响因子:6.400
doi:10.1016/j.trsl.2018.08.006
J Schlegel,J Hoffmann,D Röll,B Müller,S Günther,W Zhang,A Janise,C Vössing,B Fühler,J Neidhardt,H Khanna,B Lorenz,K Stieger