Antisense Oligonucleotide STK-002 Increases OPA1 in Retina and Improves Mitochondrial Function in Autosomal Dominant Optic Atrophy Cells
反义寡核苷酸STK-002可增加视网膜中OPA1的表达，并改善常染色体显性遗传性视神经萎缩细胞的线粒体功能。
期刊:Nucleic Acid Ther
影响因子:4.000
doi:10.1089/nat.2024.0022
Aditya Venkatesh ,Taylor McKenty ,Syed Ali ,Donna Sonntag ,Shobha Ravipaty ,Yanyan Cui ,Deirdre Slate ,Qian Lin ,Anne Christiansen ,Sarah Jacobson ,Jacob Kach ,Kian Huat Lim ,Vaishnavi Srinivasan ,Boris Zinshteyn ,Isabel Aznarez ,Laryssa A Huryn ,Zhiyu Li ,Robert B Hufnagel ,Gene Liau ,Karen Anderson ,Jeff Hoger
