An Unusual Cause of Hexokinase 1 Deficiency-Case Report

己糖激酶1缺乏症的一种罕见病因——病例报告

阅读:2

Abstract

INTRODUCTION: Molecular analysis of red cell disorders has revolutionized diagnosis, however, there remain challenges. MAIN SYMPTOMS: This patient presented with hemolytic anemia in the newborn period. He required chronic transfusions to maintain his hemoglobin level until 6 years of age. A splenectomy was performed at 3 years of age. MAIN DIAGNOSES: Using whole genome sequencing, we were able to identify a duplication upstream of the red cell promoter of HK1. Long-read RNA sequencing established aberrant expression off of this promoter. CONCLUSIONS: These non-coding variants remain challenging to identify. His promoter duplication may have a founder effect in South Asia.

特别声明

1、本页面内容包含部分的内容是基于公开信息的合理引用;引用内容仅为补充信息,不代表本站立场。

2、若认为本页面引用内容涉及侵权,请及时与本站联系,我们将第一时间处理。

3、其他媒体/个人如需使用本页面原创内容,需注明“来源:[生知库]”并获得授权;使用引用内容的,需自行联系原作者获得许可。

4、投稿及合作请联系:info@biocloudy.com。