Cellular activity of siRNA oligonucleotides containing synthetic isomorphic nucleoside surrogates

含有合成同构核苷类似物的siRNA寡核苷酸的细胞活性

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Abstract

Singly and multiply modified synthetic siRNA oligonucleotides, containing isomorphic surrogate nucleobases, show high interference potency in cell culture, suggesting the highly isomorphic RNA alphabet, based on a thieno[3,4-d]-pyrimidine core, is tolerated well by the cellular silencing machinery.

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