Fused Pyrazole Urea Analogs as Glucosylceramide Synthase Inhibitors for Treating Diseases

稠合吡唑脲类似物作为葡萄糖基神经酰胺合成酶抑制剂用于治疗疾病

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Abstract

Provided herein are novel fused pyrazole urea analogs as glucosylceramide synthase inhibitors, pharmaceutical compositions, use of such compounds in treating diseases, particularly lysosomal storage diseases, neurodegenerative diseases, cystic diseases, and cancer, and processes for preparing such compounds.

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