Familial SLC29A3-related histiocytosis with presumed choroidal infiltration: expanding the spectrum of histiocytosis-lymphadenopathy plus syndrome

家族性SLC29A3相关组织细胞增生症伴疑似脉络膜浸润:组织细胞增生症-淋巴结病附加综合征谱的扩展

阅读:3

Abstract

H syndrome (HS) is a rare autosomal recessive histiocytosis caused by biallelic mutations of the SLC29A3 gene. Ophthalmological involvement is not typical in HS, but is a known manifestation of non-Langerhans histiocytoses. We report two adult siblings with genetically confirmed HS who developed bilateral choroidal infiltration, expanding the phenotypic spectrum of SLC29A3-related histiocytosis. The first case was a woman with a history of HS who presented with progressive visual loss and choroidal lesions on imaging. Systemic findings and histological analyses confirmed non-Langerhans histiocytosis without BRAF V600E mutation. This patient's brother, who was previously asymptomatic, had similar choroidal and systemic findings. Both displayed evidence of MAPK pathway activation (phospho-ERK positive) without detectable somatic mutations. These findings expand the phenotypic spectrum of SLC29A3-related histiocytosis to include presumed choroidal involvement.

特别声明

1、本页面内容包含部分的内容是基于公开信息的合理引用;引用内容仅为补充信息,不代表本站立场。

2、若认为本页面引用内容涉及侵权,请及时与本站联系,我们将第一时间处理。

3、其他媒体/个人如需使用本页面原创内容,需注明“来源:[生知库]”并获得授权;使用引用内容的,需自行联系原作者获得许可。

4、投稿及合作请联系:info@biocloudy.com。