Case Report: 3 cases of abdominal lesions with lower limb lymphedema-rare mutations in complex lymphatic anomalies

病例报告:3例伴有下肢淋巴水肿的腹部病变——复杂淋巴异常中的罕见突变

阅读:3

Abstract

Complex lymphatic anomalies (CLAs) are rare vascular anomalies characterized by abnormal proliferation of lymphatic and blood vessels, often resulting in multisystem involvement with heterogeneous clinical manifestations. We present 3 patients with CLAs exhibiting overlapping features of lower limb lymphedema and intra-abdominal vascular malformations, a phenotypic combination infrequently described in literature. Circulating tumor DNA (ctDNA) analysis in 2 cases detected somatic mutations at significantly higher variant allele frequencies compared to population databases, and mutant genes that were previously rare in vascular diseases were reported. These noninvasive molecular findings demonstrate diagnostic utility in identifying novel genotype-phenotype associations, providing insights into disease mechanisms and informing therapeutic strategies for atypical CLAs presentations. Our observations highlight ctDNA as a promising tool for refining diagnosis and guiding personalized management in rare vascular anomalies.

特别声明

1、本页面内容包含部分的内容是基于公开信息的合理引用;引用内容仅为补充信息,不代表本站立场。

2、若认为本页面引用内容涉及侵权,请及时与本站联系,我们将第一时间处理。

3、其他媒体/个人如需使用本页面原创内容,需注明“来源:[生知库]”并获得授权;使用引用内容的,需自行联系原作者获得许可。

4、投稿及合作请联系:info@biocloudy.com。