PIK3C2B inhibition improves function and prolongs survival in myotubular myopathy animal models
PIK3C2B 抑制可改善肌管性肌病动物模型的功能并延长生存期
期刊:Journal of Clinical Investigation
影响因子:13.3
doi:10.1172/JCI86841
Nesrin Sabha, Jonathan R Volpatti, Hernan Gonorazky, Aaron Reifler, Ann E Davidson, Xingli Li, Nadine M Eltayeb, Claudia Dall'Armi, Gilbert Di Paolo, Susan V Brooks, Ana Buj-Bello, Eva L Feldman, James J Dowling