An early Transcriptomic Investigation in Adult Patients with Spinal Muscular Atrophy Under Treatment with Nusinersen.
对接受 Nusinersen 治疗的脊髓性肌萎缩症成年患者进行早期转录组学研究
期刊:Journal of Molecular Neuroscience
影响因子:2.7
doi:10.1007/s12031-024-02251-1
Liguori Maria, Bianco Annalisa, Introna Alessandro, Consiglio Arianna, Milella Giammarco, Abbatangelo Elena, D'Errico Eustachio, Licciulli Flavio, Grillo Giorgio, Simone Isabella Laura