日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

P-1779. A tale of two drugs: differential effects of sickle cell therapies on Plasmodium falciparum growth

P-1779. 两种药物的故事:镰状细胞疗法对恶性疟原虫生长的不同影响

Hsu, Shao-Yun; Ryu, Young Jae; Nepiyushchikh, Zhanna; Jeong, Kiyoung; Yu, Jinseo; Dixon, J Brandon; Kumar, Amanda; Sundararaman, Sesh A; Daley, Ellora; Ruggiero, Tonimarie; Abdulmalik, Osheiza; John, Audrey

Dissecting polycomb complexes for enhanced fetal hemoglobin production

解析多梳蛋白复合物以提高胎儿血红蛋白产量

Kaminski, Paul J; Min, Kristen; Traxler, Elizabeth A; Khandros, Eugene; Abdulmalik, Osheiza; Godfrey, Bailey; Keller, Cheryl A; Giardine, Belinda M; Hardison, Ross C; Shi, Junwei; Blobel, Gerd A

Michael Acceptor Compounds as Hemoglobin Oxygen Affinity Modulators for Reversing Sickling of Red Blood Cells

迈克尔受体化合物作为血红蛋白氧亲和力调节剂用于逆转红细胞镰状化

Mohammad, Khadijah A; Naghi, Asala H; Ghatge, Mohini S; Balogun, Benita; Macias, Mariana; Roland, Salma; Opare, Albert; Abdulmalik, Osheiza; Safo, Martin K; Omar, Abdelsattar M; El-Araby, Moustafa E

Potent Antisickling Furaldehyde Analogs for Acute Sickle Cell Therapy: Enhanced Efficacy and Intravenous Formulation Potential

用于急性镰状细胞治疗的强效抗镰状细胞糠醛类似物:增强疗效和静脉制剂潜力

Omar, Abdelsattar M; El-Araby, Moustafa E; Ahmed, Tarek A; Donkor, Akua K; Opare, Albert; Ghatge, Mohini S; Aljahdali, Anfal S; Alhashimi, Rana T; Robinson, Trevohn N; Balogun, Benita; Macias, Mariana; Roland, Salma; Zhang, Yan; Musayev, Faik N; Abdulmalik, Osheiza; Safo, Martin K

Use of HSC-targeted LNP to generate a mouse model of lethal α-thalassemia and treatment via lentiviral gene therapy

利用靶向造血干细胞的脂质纳米颗粒构建致死性α-地中海贫血小鼠模型,并通过慢病毒基因治疗进行治疗。

Chappell, Maxwell E; Breda, Laura; Tricoli, Lucas; Guerra, Amaliris; Jarocha, Danuta; Castruccio Castracani, Carlo; Papp, Tyler E; Tanaka, Naoto; Hamilton, Nolan; Triebwasser, Michael P; Ghiaccio, Valentina; Fedorky, Megan T; Gollomp, Kandace L; Bochenek, Veronica; Roche, Aoife M; Everett, John K; Cook, Emma J; Bushman, Frederic D; Teawtrakul, Nattiya; Glentis, Stavros; Kattamis, Antonis; Mui, Barbara L; Tam, Ying K; Weissman, Drew; Abdulmalik, Osheiza; Parhiz, Hamideh; Rivella, Stefano

The antisickling agent, 5-hydroxymethyl-2-furfural: Other potential pharmacological applications

抗镰状细胞贫血剂5-羟甲基-2-糠醛:其他潜在的药理学应用

Pagare, Piyusha P; McGinn, Mina; Ghatge, Mohini S; Shekhar, Vibha; Alhashimi, Rana T; Daniel Pierce, B; Abdulmalik, Osheiza; Zhang, Yan; Safo, Martin K

Modeling primitive and definitive erythropoiesis with induced pluripotent stem cells

利用诱导多能干细胞模拟原始和终末红细胞生成

Pavani, Giulia; Klein, Joshua G; Nations, Catriana C; Sussman, Jonathan H; Tan, Kai; An, Hyun Hyung; Abdulmalik, Osheiza; Thom, Christopher S; Gearhart, Peter A; Willett, Camryn M; Maguire, Jean Ann; Chou, Stella T; French, Deborah L; Gadue, Paul

Optimizing the lyophilization of Lumbricus terrestris erythrocruorin.

优化蚯蚓红细胞冻干工艺

Dowd Sean, Sharo Catherine, Abdulmalik Osheiza, Elmer Jacob

Targeted modification of furan-2-carboxaldehydes into Michael acceptor analogs yielded long-acting hemoglobin modulators with dual antisickling activities

将呋喃-2-甲醛靶向修饰为迈克尔受体类似物,可得到具有双重抗镰状细胞活性的长效血红蛋白调节剂。

Omar, Abdelsattar M; Abdulmalik, Osheiza; El-Say, Khalid M; Ghatge, Mohini S; Cyril-Olutayo, Mojisola; Paredes, Steven; Al-Awadh, Mohammed; El-Araby, Moustafa E; Safo, Martin K

In vivo hematopoietic stem cell modification by mRNA delivery

通过mRNA递送对体内造血干细胞进行修饰

Breda, Laura; Papp, Tyler E; Triebwasser, Michael P; Yadegari, Amir; Fedorky, Megan T; Tanaka, Naoto; Abdulmalik, Osheiza; Pavani, Giulia; Wang, Yongping; Grupp, Stephan A; Chou, Stella T; Ni, Houping; Mui, Barbara L; Tam, Ying K; Weissman, Drew; Rivella, Stefano; Parhiz, Hamideh