Relationship between age at initiation of cysteamine treatment, adherence with therapy, and glomerular kidney function in infantile nephropathic cystinosis
婴儿肾病胱氨酸病中开始使用半胱胺治疗的年龄、治疗依从性与肾小球肾功能之间的关系
期刊:Molecular Genetics and Metabolism
影响因子:3.5
doi:10.1016/j.ymgme.2022.06.010
Nießl, Christina; Boulesteix, Anne-Laure; Oh, Jun; Palm, Katja; Schlingmann, Peter; Wygoda, Simone; Haffner, Dieter; Wühl, Elke; Tönshoff, Burkhard; Buescher, Anja; Billing, Heiko; Hoppe, Bernd; Zirngibl, Matthias; Kettwig, Matthias; Moeller, Kristina; Acham-Roschitz, Birgit; Arbeiter, Klaus; Bald, Martin; Benz, Marcus; Galiano, Matthias; John-Kroegel, Ulrike; Klaus, Guenter; Marx-Berger, Daniela; Moser, Katja; Mueller, Dirk; Patzer, Ludwig; Pohl, Martin; Seitz, Barbara; Treikauskas, Ulrike; von Vigier, Rodo O; Gahl, William Allen; Hohenfellner, Katharina