Genetic correction of HAX1 in induced pluripotent stem cells from a patient with severe congenital neutropenia improves defective granulopoiesis
对患有严重先天性中性粒细胞减少症的患者的诱导性多能干细胞中的 HAX1 进行基因校正可改善缺陷的粒细胞生成
期刊:Haematologica
影响因子:8.2
doi:10.3324/haematol.2013.083873
Tatsuya Morishima, Ken-ichiro Watanabe, Akira Niwa, Hideyo Hirai, Satoshi Saida, Takayuki Tanaka, Itaru Kato, Katsutsugu Umeda, Hidefumi Hiramatsu, Megumu K Saito, Kousaku Matsubara, Souichi Adachi, Masao Kobayashi, Tatsutoshi Nakahata, Toshio Heike