From bench to bedside: Improving the clinical safety of GalNAc-siRNA conjugates using seed-pairing destabilization
从实验室到临床:利用种子配对不稳定提高 GalNAc-siRNA 结合物的临床安全性
期刊:Nucleic Acids Research
影响因子:16.6
doi:10.1093/nar/gkac539
Mark K Schlegel, Maja M Janas, Yongfeng Jiang, Joseph D Barry, Wendell Davis, Saket Agarwal, Daniel Berman, Christopher R Brown, Adam Castoreno, Sarah LeBlanc, Abigail Liebow, Tara Mayo, Stuart Milstein, Tuyen Nguyen, Svetlana Shulga-Morskaya, Sarah Hyde, Sally Schofield, John Szeto, Lauren Blair Wo