日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Clinical Efficacy of ONC201 in H3K27M-Mutant Diffuse Midline Gliomas Is Driven by Disruption of Integrated Metabolic and Epigenetic Pathways

ONC201治疗H3K27M突变型弥漫性中线胶质瘤的临床疗效是由整合代谢和表观遗传通路紊乱驱动的

Sriram Venneti # ,Abed Rahman Kawakibi # ,Sunjong Ji # ,Sebastian M Waszak # ,Stefan R Sweha # ,Mateus Mota # ,Matthew Pun # ,Akash Deogharkar ,Chan Chung ,Rohinton S Tarapore ,Samuel Ramage ,Andrew Chi ,Patrick Y Wen ,Isabel Arrillaga-Romany ,Tracy T Batchelor ,Nicholas A Butowski ,Ashley Sumrall ,Nicole Shonka ,Rebecca A Harrison ,John de Groot ,Minesh Mehta ,Matthew D Hall ,Doured Daghistani ,Timothy F Cloughesy ,Benjamin M Ellingson ,Kevin Beccaria ,Pascale Varlet ,Michelle M Kim ,Yoshie Umemura ,Hugh Garton ,Andrea Franson ,Jonathan Schwartz ,Rajan Jain ,Maureen Kachman ,Heidi Baum ,Charles F Burant ,Sophie L Mottl ,Rodrigo T Cartaxo ,Vishal John ,Dana Messinger ,Tingting Qin ,Erik Peterson ,Peter Sajjakulnukit ,Karthik Ravi ,Alyssa Waugh ,Dustin Walling ,Yujie Ding ,Ziyun Xia ,Anna Schwendeman ,Debra Hawes ,Fusheng Yang ,Alexander R Judkins ,Daniel Wahl ,Costas A Lyssiotis ,Daniel de la Nava ,Marta M Alonso ,Augustine Eze ,Jasper Spitzer ,Susanne V Schmidt ,Ryan J Duchatel ,Matthew D Dun ,Jason E Cain ,Li Jiang ,Sylwia A Stopka ,Gerard Baquer ,Michael S Regan ,Mariella G Filbin ,Nathalie Y R Agar ,Lili Zhao ,Chandan Kumar-Sinha ,Rajen Mody ,Arul Chinnaiyan ,Ryo Kurokawa ,Drew Pratt ,Viveka N Yadav ,Jacques Grill ,Cassie Kline ,Sabine Mueller ,Adam Resnick ,Javad Nazarian ,Joshua E Allen ,Yazmin Odia ,Sharon L Gardner ,Carl Koschmann

The landscape of tumor cell states and spatial organization in H3-K27M mutant diffuse midline glioma across age and location

H3-K27M突变型弥漫性中线胶质瘤在不同年龄和部位的肿瘤细胞状态和空间组织结构

Ilon Liu # ,Li Jiang # ,Erik R Samuelsson # ,Sergio Marco Salas ,Alexander Beck ,Olivia A Hack ,Daeun Jeong ,McKenzie L Shaw ,Bernhard Englinger ,Jenna LaBelle ,Hafsa M Mire ,Sibylle Madlener ,Lisa Mayr ,Michael A Quezada ,Maria Trissal ,Eshini Panditharatna ,Kati J Ernst ,Jayne Vogelzang ,Taylor A Gatesman ,Matthew E Halbert ,Hana Palova ,Petra Pokorna ,Jaroslav Sterba ,Ondrej Slaby ,Rene Geyeregger ,Aaron Diaz ,Izac J Findlay ,Matthew D Dun ,Adam Resnick ,Mario L Suvà ,David T W Jones ,Sameer Agnihotri ,Jessica Svedlund ,Carl Koschmann ,Christine Haberler ,Thomas Czech ,Irene Slavc ,Jennifer A Cotter ,Keith L Ligon ,Sanda Alexandrescu ,W K Alfred Yung ,Isabel Arrillaga-Romany ,Johannes Gojo ,Michelle Monje ,Mats Nilsson ,Mariella G Filbin

MODL-28. Patient-derived, three-dimensional organoid platform for pediatric brain tumor modeling

MODL-28:用于儿童脑肿瘤建模的患者来源三维类器官平台

Kato, Tomohisa Jr; Muotri, Alysson R; Maeda, Sachi; Ohka, Fumiharu; Kanamori, Fumiaki; Okumura, Yuka; Takeuchi, Kazuhito; Nagata, Yuichi; Yamaguchi, Junya; Harada, Hideyuki; Shimizu, Hiroki; Takido, Yuhei; Saito, Ryuta; Barathi, Bhargavi Brahmendra; Malgulwar, Prit; Liu, Yang; Kannan, Kasthuri; Huse, Jason; Chen, Y; Bax, S; Prior, V; Hsu, K; Kramer, B; Goodhand, T; MacLeod, J; McCowage, G; Gore, S; Gowrishankar, K; O’Neill, G; Baubet, Valerie; Beale, David; Mariarita, Santi; Viaene, Angela; Madsen, Peter; Jacob, Fadi; Ming, Guo-li; Hongjun, Song; Phillip, Storm; Koptyra, Mateusz; Adam, Resnick

Discovery and functional characterization of the oncogenicity and targetability of a novel NOTCH1-ROS1 gene fusion in pediatric angiosarcoma

儿童血管肉瘤中新型 NOTCH1-ROS1 基因融合的致癌性和靶向性的发现及功能表征

Payal Jain, Sudarshan Iyer, Joshua Straka, Lea F Surrey, Jennifer Pogoriler, Harry Han, Tiffany Smith, Christine Busch, Elizabeth Fox, Marilyn Li, Angela J Waanders, Adam Resnick #, Monika A Davare #

Integrated Molecular Meta-Analysis of 1,000 Pediatric High-Grade and Diffuse Intrinsic Pontine Glioma

对1000例儿童高级别和弥漫性内生性脑桥胶质瘤进行综合分子荟萃分析

Alan Mackay ,Anna Burford ,Diana Carvalho ,Elisa Izquierdo ,Janat Fazal-Salom ,Kathryn R Taylor ,Lynn Bjerke ,Matthew Clarke ,Mara Vinci ,Meera Nandhabalan ,Sara Temelso ,Sergey Popov ,Valeria Molinari ,Pichai Raman ,Angela J Waanders ,Harry J Han ,Saumya Gupta ,Lynley Marshall ,Stergios Zacharoulis ,Sucheta Vaidya ,Henry C Mandeville ,Leslie R Bridges ,Andrew J Martin ,Safa Al-Sarraj ,Christopher Chandler ,Ho-Keung Ng ,Xingang Li ,Kun Mu ,Saoussen Trabelsi ,Dorra H'mida-Ben Brahim ,Alexei N Kisljakov ,Dmitry M Konovalov ,Andrew S Moore ,Angel Montero Carcaboso ,Mariona Sunol ,Carmen de Torres ,Ofelia Cruz ,Jaume Mora ,Ludmila I Shats ,João N Stavale ,Lucas T Bidinotto ,Rui M Reis ,Natacha Entz-Werle ,Michael Farrell ,Jane Cryan ,Darach Crimmins ,John Caird ,Jane Pears ,Michelle Monje ,Marie-Anne Debily ,David Castel ,Jacques Grill ,Cynthia Hawkins ,Hamid Nikbakht ,Nada Jabado ,Suzanne J Baker ,Stefan M Pfister ,David T W Jones ,Maryam Fouladi ,André O von Bueren ,Michael Baudis ,Adam Resnick ,Chris Jones