日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Engineered Cas9 variants bypass Keap1-mediated degradation in human cells and enhance epigenome editing efficiency

经过基因工程改造的Cas9变体可绕过Keap1介导的降解,从而提高人类细胞中的表观基因组编辑效率。

Jianfeng Chen ,Siyuan Su ,Adrian Pickar-Oliver ,Anna M Chiarella ,Quentin Hahn ,Dennis Goldfarb ,Erica W Cloer ,George W Small ,Smaran Sivashankar ,Dale A Ramsden ,Michael B Major ,Nathaniel A Hathaway ,Charles A Gersbach ,Pengda Liu

Branched-chain α-ketoacids are preferentially reaminated and activate protein synthesis in the heart

支链 α-酮酸优先被重新胺化并激活心脏中的蛋白质合成

Jacquelyn M Walejko #, Bridgette A Christopher #, Scott B Crown #, Guo-Fang Zhang, Adrian Pickar-Oliver, Takeshi Yoneshiro, Matthew W Foster, Stephani Page, Stephan van Vliet, Olga Ilkayeva, Michael J Muehlbauer, Matthew W Carson, Joseph T Brozinick, Craig D Hammond, Ruth E Gimeno, M Arthur Moseley,

Full-length dystrophin restoration via targeted exon integration by AAV-CRISPR in a humanized mouse model of Duchenne muscular dystrophy

在杜氏肌营养不良症人源化小鼠模型中,通过 AAV-CRISPR 靶向外显子整合实现全长肌营养不良蛋白修复

Adrian Pickar-Oliver, Veronica Gough, Joel D Bohning, Siyan Liu, Jacqueline N Robinson-Hamm, Heather Daniels, William H Majoros, Garth Devlin, Aravind Asokan, Charles A Gersbach

Redirecting Vesicular Transport to Improve Nonviral Delivery of Molecular Cargo

重定向囊泡运输以改善分子货物的非病毒运送

Mao Mao, Chun-Chi Chang, Adrian Pickar-Oliver, Lisa D Cervia, Liangli Wang, Jing Ji, Paloma B Liton, Charles A Gersbach, Fan Yuan

Targeted transcriptional modulation with type I CRISPR-Cas systems in human cells

使用 I 型 CRISPR-Cas 系统在人类细胞中进行靶向转录调控

Adrian Pickar-Oliver, Joshua B Black, Mae M Lewis, Kevin J Mutchnick, Tyler S Klann, Kylie A Gilcrest, Madeleine J Sitton, Christopher E Nelson, Alejandro Barrera, Luke C Bartelt, Timothy E Reddy, Chase L Beisel, Rodolphe Barrangou, Charles A Gersbach

Mumps Virus Nucleoprotein Enhances Phosphorylation of the Phosphoprotein by Polo-Like Kinase 1

腮腺炎病毒核蛋白通过 Polo 样激酶 1 增强磷蛋白的磷酸化

Adrian Pickar, James Zengel, Pei Xu, Zhuo Li, Biao He

Roles of serine and threonine residues of mumps virus P protein in viral transcription and replication

腮腺炎病毒P蛋白丝氨酸和苏氨酸残基在病毒转录和复制中的作用

Adrian Pickar, Pei Xu, Andrew Elson, Zhuo Li, James Zengel, Biao He