日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Introducing iCatalog as a clinical decision support tool for collaborative pediatric precision oncology studies

介绍 iCatalog,它是一款用于协作式儿科精准肿瘤学研究的临床决策支持工具。

Kang, Wenjun; Lazo de la Vega, Lorena; Comeau, Hannah; Agastra, Ergina; Maese, Luke D; Kim, AeRang; Sukharevsky, Ellen; Ceca, Evelina; Corson, Laura; White, Joseph; Weiser, Daniel A; Applebaum, Mark A; Colace, Susan I; Chen, Mengjie; Johnson, Julie A; Volchenboum, Samuel; Pinto, Navin R; Church, Alanna J; Janeway, Katherine A

A Phase 1/2 Study of Lenvatinib in Combination With Everolimus in Recurrent and Refractory Pediatric and Young Adult Solid Tumors

乐伐替尼联合依维莫司治疗复发性和难治性儿童及青少年实体瘤的1/2期研究

Dela Cruz, Filemon S; Fox, Elizabeth; DuBois, Steven G; Friedman, Gregory K; Croop, James M; Kim, AeRang; Morgenstern, Daniel A; Balis, Frank M; Macy, Margaret E; Pressey, Joseph G; Watt, Tanya; Krystal, Julie I; Vo, Kieuhoa T; Mody, Rajen; Laetsch, Theodore W; Weigel, Brenda J; O'Hara, Karen; He, Cixin S; Aluri, Jagadeesh; Okpara, Chinyere E; Glade Bender, Julia L

Open-Label, Multicenter, Phase I/II, First-in-Human Trial of TK216: A First-Generation EWS::FLI1 Fusion Protein Antagonist in Ewing Sarcoma

TK216 的开放标签、多中心、I/II 期、首次人体试验:一种治疗尤文氏肉瘤的第一代 EWS::FLI1 融合蛋白拮抗剂

Meyers, Paul A; Federman, Noah; Daw, Najat; Anderson, Peter M; Davis, Lara E; Kim, AeRang; Macy, Margaret E; Pietrofeso, Angela; Ratan, Ravin; Riedel, Richard F; Trucco, Matteo; Breitmeyer, James B; Toretsky, Jeffrey A; Ludwig, Joseph A

Early Detection of Malignant and Premalignant Peripheral Nerve Tumors Using Cell-Free DNA Fragmentomics

利用无细胞DNA片段组学早期检测恶性及癌前周围神经肿瘤

Sundby, R Taylor; Szymanski, Jeffrey J; Pan, Alexander C; Jones, Paul A; Mahmood, Sana Z; Reid, Olivia H; Srihari, Divya; Armstrong, Amy E; Chamberlain, Stacey; Burgic, Sanita; Weekley, Kara; Murray, Béga; Patel, Sneh; Qaium, Faridi; Lucas, Andrea N; Fagan, Margaret; Dufek, Anne; Meyer, Christian F; Collins, Natalie B; Pratilas, Christine A; Dombi, Eva; Gross, Andrea M; Kim, AeRang; Chrisinger, John S A; Dehner, Carina A; Widemann, Brigitte C; Hirbe, Angela C; Chaudhuri, Aadel A; Shern, Jack F

Phase II study of vemurafenib in children and young adults with tumors harboring BRAF V600 mutations: NCI-COG pediatric MATCH trial (APEC1621) Arm G

一项针对携带 BRAF V600 突变的肿瘤儿童和青少年的维莫非尼 II 期研究:NCI-COG 儿科 MATCH 试验 (APEC1621) G 组

Nelson, Marie V; Kim, AeRang; Williams, P Mickey; Roy-Chowdhuri, Sinchita; Patton, David R; Coffey, Brent D; Reid, Joel M; Piao, Jin; Saguilig, Lauren; Alonzo, Todd A; Berg, Stacey L; Ramirez, Nilsa C; Jaju, Alok; Fox, Elizabeth; Weigel, Brenda J; Hawkins, Douglas S; Mooney, Margaret M; Takebe, Naoko; Tricoli, James V; Janeway, Katherine A; Seibel, Nita L; Parsons, D Williams

Platform trial design for neurofibromatosis type 1, NF2-related schwannomatosis and non-NF2-related schwannomatosis: A potential model for rare diseases

针对1型神经纤维瘤病、NF2相关神经鞘瘤病和非NF2相关神经鞘瘤病的平台试验设计:一种潜在的罕见病模型

Dhaenens, Britt A E; Heimann, Günter; Bakker, Annette; Nievo, Marco; Ferner, Rosalie E; Evans, D Gareth; Wolkenstein, Pierre; Leubner, Jonas; Potratz, Cornelia; Carton, Charlotte; Iloeje, Uchenna; Kirk, George; Blakeley, Jaishri O; Plotkin, Scott; Fisher, Michael J; Kim, AeRang; Driever, Pablo Hernáiz; Azizi, Amedeo A; Widemann, Brigitte C; Gross, Andrea; Parke, Tom; Legius, Eric; Oostenbrink, Rianne

Recommendations for the collection and annotation of biosamples for analysis of biomarkers in neurofibromatosis and schwannomatosis clinical trials

神经纤维瘤病和神经鞘瘤病临床试验中生物标志物分析所需生物样本的收集和注释建议

Sundby, R Taylor; Rhodes, Steven D; Komlodi-Pasztor, Edina; Sarnoff, Herb; Grasso, Vito; Upadhyaya, Meena; Kim, AeRang; Evans, D Gareth; Blakeley, Jaishri O; Hanemann, C Oliver; Bettegowda, Chetan

Early detection of malignant and pre-malignant peripheral nerve tumors using cell-free DNA fragmentomics

利用无细胞DNA片段组学早期检测恶性及癌前周围神经肿瘤

Taylor Sundby, R; Szymanski, Jeffrey J; Pan, Alexander; Jones, Paul A; Mahmood, Sana Z; Reid, Olivia H; Srihari, Divya; Armstrong, Amy E; Chamberlain, Stacey; Burgic, Sanita; Weekley, Kara; Murray, Béga; Patel, Sneh; Qaium, Faridi; Lucas, Andrea N; Fagan, Margaret; Dufek, Anne; Meyer, Christian F; Collins, Natalie B; Pratilas, Christine A; Dombi, Eva; Gross, Andrea M; Kim, AeRang; Chrisinger, John S A; Dehner, Carina A; Widemann, Brigitte C; Hirbe, Angela C; Chaudhuri, Aadel A; Shern, Jack F

Long-term safety and efficacy of selumetinib in children with neurofibromatosis type 1 on a phase 1/2 trial for inoperable plexiform neurofibromas

一项针对无法手术切除的丛状神经纤维瘤患儿的 1/2 期临床试验,评估了 selumetinib 在 1 型神经纤维瘤病患儿中的长期安全性和有效性

Gross, Andrea M; Dombi, Eva; Wolters, Pamela L; Baldwin, Andrea; Dufek, Anne; Herrera, Kailey; Martin, Staci; Derdak, Joanne; Heisey, Kara S; Whitcomb, Patricia M; Steinberg, Seth M; Venzon, David J; Fisher, Michael J; Kim, AeRang; Bornhorst, Miriam; Weiss, Brian D; Blakeley, Jaishri O; Smith, Malcolm A; Widemann, Brigitte C

Clinical Targeted Next-Generation Panel Sequencing Reveals MYC Amplification Is a Poor Prognostic Factor in Osteosarcoma

临床靶向二代测序揭示MYC扩增是骨肉瘤预后不良因素

Marinoff, Amanda E; Spurr, Liam F; Fong, Christina; Li, Yvonne Y; Forrest, Suzanne J; Ward, Abigail; Doan, Duong; Corson, Laura; Mauguen, Audrey; Pinto, Navin; Maese, Luke; Colace, Susan; Macy, Margaret E; Kim, AeRang; Sabnis, Amit J; Applebaum, Mark A; Laetsch, Theodore W; Glade-Bender, Julia; Weiser, Daniel A; Anderson, Megan; Crompton, Brian D; Meyers, Paul; Zehir, Ahmet; MacConaill, Laura; Lindeman, Neal; Nowak, Jonathan A; Ladanyi, Marc; Church, Alanna J; Cherniack, Andrew D; Shukla, Neerav; Janeway, Katherine A