日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Enhancing lentiviral production for WAS gene therapy: a comparative analysis of stable producer cell lines evaluating flatware system and adherent bioreactors in perfusion mode

提高慢病毒产量以用于WAS基因治疗:稳定生产细胞系在灌流模式下对平板系统和贴壁生物反应器的比较分析

Singh, Parameswari; Lal, Nikki Indresh; Terrao, Monica; Schwingal, Sarah; Biserni, Martina; Aeschimann, Florian; Strauch, Andrea; Dersch, Herbert; Jaramillo, Angel; Gille, Andreas; Laux, Holger

An optimized protocol for quality control of gene therapy vectors using nanopore direct RNA sequencing

一种利用纳米孔直接RNA测序进行基因治疗载体质量控制的优化方案

Zeglinski, Kathleen; Montellese, Christian; Ritchie, Matthew E; Alhamdoosh, Monther; Vonarburg, Cédric; Bowden, Rory; Jordi, Monika; Gouil, Quentin; Aeschimann, Florian; Hsu, Arthur

DNA-PK inhibition enhances gene editing efficiency in HSPCs for CRISPR-based treatment of X-linked hyper IgM syndrome.

DNA-PK 抑制剂可提高 HSPC 中基因编辑的效率,从而利用 CRISPR 技术治疗 X 连锁高 IgM 综合征

Pugliano Cole M, Berger Mason, Ray Roslyn M, Sapkos Kai, Wu Betty, Laird Aidan, Ye Yidian, Thomson Daniel, DeGottardi M Quinn, Khan Iram F, Tatiossian Kristina, Miles Brodie A, Aeschimann Florian, Pasquier Jerome, Kim Mihee M, Rawlings David J

Timing mechanism of sexually dimorphic nervous system differentiation

性二态性神经系统分化的时间机制

Pereira, Laura; Aeschimann, Florian; Wang, Chen; Lawson, Hannah; Serrano-Saiz, Esther; Portman, Douglas S; Großhans, Helge; Hobert, Oliver

let-7 coordinates the transition to adulthood through a single primary and four secondary targets

let-7 通过一个主要靶点和四个次要靶点协调向成年的过渡。

Aeschimann, Florian; Neagu, Anca; Rausch, Magdalene; Großhans, Helge

Structural basis of siRNA recognition by TRBP double-stranded RNA binding domains

TRBP双链RNA结合域识别siRNA的结构基础

Masliah, Gregoire; Maris, Christophe; König, Sebastian Lb; Yulikov, Maxim; Aeschimann, Florian; Malinowska, Anna L; Mabille, Julie; Weiler, Jan; Holla, Andrea; Hunziker, Juerg; Meisner-Kober, Nicole; Schuler, Benjamin; Jeschke, Gunnar; Allain, Frederic H-T

Bayesian prediction of RNA translation from ribosome profiling

基于核糖体谱的RNA翻译贝叶斯预测

Malone, Brandon; Atanassov, Ilian; Aeschimann, Florian; Li, Xinping; Großhans, Helge; Dieterich, Christoph