日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Primary Lateral Sclerosis Natural History Study: Primary Lateral Sclerosis Functional Rating Scale and Other Outcomes Assessment

原发性侧索硬化症自然史研究:原发性侧索硬化症功能评定量表及其他结局评估

Lee, Ikjae; Jang, Grace; Cheung, Ying Kuen Ken; Sherman, Alexander V; Johnston, Wendy S; Diaz, Frank; Fernandes, J Americo M; Habib, Ali A; Maragakis, Nicholas J; Paganoni, Sabrina; Burke, Katherine; Oskarsson, Bjorn; Shah, Jaimin; Zinman, Lorne; Floeter, Mary Kay; Ajroud-Driss, Senda; Gwathmey, Kelly; Heiman-Patterson, Terry; Jawdat, Omar; Kasarskis, Edward J; Kisanuki, Yaz Y; Wymer, James; Fournier, Christina; Hayat, Ghazala; Heitzman, Daragh; Lomen-Hoerth, Catherine; Pulley, Michael T; Scelsa, Stephen N; Walk, David; Goutman, Stephen A; Shoesmith, Christen; Simmons, Zachary; Sorenson, Eric; Elman, Lauren; Harms, Matthew B; Hoover, Benjamin N; Yun, Rebecca Y; Santella, Regina M; Mitsumoto, Hiroshi

Dynamics of Nerve Conduction Studies in Patients With Guillain-Barré Syndrome

格林-巴利综合征患者神经传导研究的动态变化

Arends, Samuel; de Koning, Laura; Drenthen, Judith; Zhu, Mahova; van den Bergh, Peter Y K; Hadden, Robert M; Shahrizaila, Nortina; Reisin, Ricardo C; Kuwabara, Satoshi; Ajroud-Driss, Senda; Antonini, Giovanni; Balducci, Claudia; Barroso, Fabio A; Brannagan, Thomas H; Buermann, Jan; Casasnovas, Carlos; Cavaletti, Guido; Chao, Chi-Chao; Dillmann, Ulrich; Dimachkie, Mazen M; Galassi, Giuliana; Gutiérrez-Gutiérrez, Gerardo; Harbo, Thomas; Hsieh, Sung-Tsang; Islam, Badrul; Katzberg, Hans; Kiers, Lynette; Mataluni, Giorgia; Pardo, Julio; Peréon, Yann; Rajabally, Yusuf A; Stettner, Mark; Verhamme, Camiel; Vytopil, Michal; Waqar, Waheed; Cornblath, David R; Jacobs, Bart C

CNM-Au8 in Amyotrophic Lateral Sclerosis: The HEALEY ALS Platform Trial

CNM-Au8 在肌萎缩侧索硬化症中的应用:HEALEY ALS 平台试验

Berry, James D; Maragakis, Nicholas J; Macklin, Eric A; Chibnik, Lori B; Quintana, Melanie; Saville, Benjamin R; Detry, Michelle A; Vestrucci, Matteo; Marion, Joseph; McGlothlin, Anna; Stommel, Elijah W; Chase, Marianne; Pothier, Lindsay; Harkey, Brittney A; Yu, Hong; Sherman, Alex; Shefner, Jeremy; Hall, Meghan; Kittle, Gale; Babu, Suma; Andrews, Jinsy; D'Agostino, Derek; Tustison, Eric; Scirocco, Erica; Giacomelli, Elisa; Alameda, Gustavo; Locatelli, Eduardo; Ho, Doreen; Quick, Adam; Ajroud-Driss, Senda; Katz, Jonathan; Heitzman, Daragh; Appel, Stanley H; Shroff, Sheetal; Felice, Kevin J; Simmons, Zachary; Miller, Timothy; Olney, Nicholas; Weiss, Michael D; Goutman, Stephen A; Fernandes, Joseph Americo Jr; Jawdat, Omar; Owegi, Margaret Ayo; Foster, Laura; Vu, Tuan; Ilieva, Hristelina; Newman, Daniel S; Arcila-Londono, Ximena; Jackson, Carlayne; Ladha, Shafeeq; Heiman-Patterson, Terry; Caress, James; Swenson, Andrea; Peltier, Amanda; Lewis, Richard; Fee, Dominic; Elliott, Matthew; Bedlack, Richard; Kasarskis, Edward J; Elman, Lauren; Rosenfeld, Jeffrey; Walk, David; McIlduff, Courtney E; Twydell, Paul; Young, Eufrosina; Johnson, Kristin; Rezania, Kourosh; Goyal, Namita A; Cohen, Jeffrey A; Benatar, Michael; Jones, Vovanti; Glass, Jonathan; Shah, Jaimin; Beydoun, Said R; Wymer, James P; Zilliox, Lindsay; Nayar, Shakti; Pattee, Gary L; Martinez-Thompson, Jennifer; Rynders, Austin; Evan, Jacob; Evan, Jeremy; Hartford, Alan; Sepassi, Marjan; Ho, Karen S; Glanzman, Robert; Greenberg, Benjamin; Hotchkin, Michael T; Paganoni, Sabrina; Cudkowicz, Merit E

Pridopidine in Amyotrophic Lateral Sclerosis: The HEALEY ALS Platform Trial

普利多吡啶治疗肌萎缩侧索硬化症:HEALEY ALS平台试验

Shefner, Jeremy M; Oskarsson, Björn; Macklin, Eric A; Chibnik, Lori B; Quintana, Melanie; Saville, Benjamin R; Detry, Michelle A; Vestrucci, Matteo; Marion, Joe; McGlothlin, Anna; Heiman-Patterson, Terry; Chase, Marianne; Pothier, Lindsay; Harkey, Brittney A; Yu, Hong; Sherman, Alexander V; Hall, Meghan; Kittle, Gale; Berry, James D; Babu, Suma; Andrews, Jinsy; D'Agostino, Derek; Tustison, Eric; Scirocco, Erica; Giacomelli, Elisa; Alameda, Gustavo; Locatelli, Eduardo; Ho, Doreen; Quick, Adam; Ajroud-Driss, Senda; Katz, Jonathan; Heitzman, Daragh; Appel, Stanley H; Shroff, Sheetal; Felice, Kevin; Maragakis, Nicholas J; Simmons, Zachary; Miller, Timothy M; Olney, Nicholas; Weiss, Michael D; Goutman, Stephen A; Fernandes, Joseph Americo; Jawdat, Omar; Owegi, Margaret Ayo; Foster, Laura A; Vu, Tuan; Ilieva, Hristelina; Newman, Daniel S; Arcila-Londono, Ximena; Jackson, Carlayne E; Ladha, Shafeeq; Caress, James B; Swenson, Andrea; Peltier, Amanda; Lewis, Richard A; Fee, Dominic; Elliott, Matthew; Bedlack, Richard; Kasarskis, Edward J; Elman, Lauren; Rosenfeld, Jeffrey; Walk, David; McIlduff, Courtney; Twydell, Paul; Young, Eufrosina; Johnson, Kristin; Rezania, Kourosh; Goyal, Namita A; Cohen, Jeffrey A; Benatar, Michael; Jones, Vovanti; Shah, Jaimin; Beydoun, Said R; Wymer, James P; Zilliox, Lindsay; Nayar, Shakti; Pattee, Gary L; Martinez-Thompson, Jennifer; Leitner, Melanie L; Chen, Kelly; Goldberg, Y Paul; Cohen, Yael; Geva, Michal; Hayden, Michael R; Paganoni, Sabrina; Cudkowicz, Merit E

Verdiperstat in Amyotrophic Lateral Sclerosis: Results From the Randomized HEALEY ALS Platform Trial

Verdiperstat治疗肌萎缩侧索硬化症:来自随机HEALEY ALS平台试验的结果

Andrews, Jinsy; Paganoni, Sabrina; Macklin, Eric A; Chibnik, Lori B; Quintana, Melanie; Saville, Benjamin R; Detry, Michelle A; Vestrucci, Matteo; Marion, Joseph; McGlothlin, Anna; Young, Eufrosina; Chase, Marianne; Pothier, Lindsay; Harkey, Brittney; Yu, Hong; Sherman, Alex; Shefner, Jeremy; Hall, Meghan; Kittle, Gale; Connolly, Mariah R; Berry, James D; D'Agostino, Derek; Tustison, Eric; Giacomelli, Elisa; Scirocco, Erica; Alameda, Gustavo; Locatelli, Eduardo; Ho, Doreen; Quick, Adam; Heitzman, Daragh; Ajroud-Driss, Senda; Appel, Stanley H; Shroff, Sheetal; Katz, Jonathan; Felice, Kevin; Maragakis, Nicholas J; Simmons, Zachary; Goutman, Stephen A; Olney, Nicholas; Miller, Timothy; Fernandes, Joseph Americo; Ilieva, Hristelina; Jawdat, Omar; Weiss, Michael D; Foster, Laura; Vu, Tuan; Ladha, Shafeeq; Owegi, Margaret Ayo; Newman, Daniel S; Arcila-Londono, Ximena; Jackson, Carlayne E; Swenson, Andrea; Heiman-Patterson, Terry; Caress, James; Fee, Dominic; Peltier, Amanda; Lewis, Richard; Rosenfeld, Jeffrey; Walk, David; Johnson, Kristin; Elliott, Matthew; Kasarskis, Edward J; Rutkove, Seward; McIlduff, Courtney E; Bedlack, Richard; Elman, Lauren; Goyal, Namita A; Rezania, Kourosh; Twydell, Paul; Benatar, Michael; Glass, Jonathan; Cohen, Jeffrey A; Jones, Vovanti; Zilliox, Lindsay; Wymer, James P; Beydoun, Said R; Shah, Jaimin; Pattee, Gary L; Martinez-Thompson, Jennifer; Nayar, Shakti; Granit, Volkan; Donohue, Mary; Grossman, Katheryn; Campbell, Daniel J; Qureshi, Irfan A; Cudkowicz, Merit E; Babu, Suma

Efficacy and Safety of Zilucoplan in Amyotrophic Lateral Sclerosis: A Randomized Clinical Trial

Zilucoplan治疗肌萎缩侧索硬化症的疗效和安全性:一项随机临床试验

Paganoni, Sabrina; Fournier, Christina N; Macklin, Eric A; Chibnik, Lori B; Quintana, Melanie; Saville, Benjamin R; Detry, Michelle A; Vestrucci, Matteo; Marion, Joe; McGlothlin, Anna; Ajroud-Driss, Senda; Chase, Marianne; Pothier, Lindsay; Harkey, Brittney A; Yu, Hong; Sherman, Alexander V; Shefner, Jeremy M; Hall, Meghan; Kittle, Gale; Berry, James D; Babu, Suma; Andrews, Jinsy; Dagostino, Derek; Tustison, Eric; Giacomelli, Elisa; Scirocco, Erica; Alameda, Gustavo; Locatelli, Eduardo; Ho, Doreen; Quick, Adam; Katz, Jonathan; Heitzman, Daragh; Appel, Stanley H; Shroff, Sheetal; Felice, Kevin; Maragakis, Nicholas J; Simmons, Zachary; Miller, Timothy M; Olney, Nicholas; Weiss, Michael D; Goutman, Stephen A; Fernandes, Joseph Americo; Jawdat, Omar; Owegi, Margaret Ayo; Foster, Laura A; Vu, Tuan; Ilieva, Hristelina; Newman, Daniel S; Arcila-Londono, Ximena; Jackson, Carlayne E; Ladha, Shafeeq; Heiman-Patterson, Terry; Caress, James B; Swenson, Andrea; Peltier, Amanda; Lewis, Richard; Fee, Dominic; Elliott, Matthew; Bedlack, Richard; Kasarskis, Edward J; Elman, Lauren; Rosenfeld, Jeffrey; Walk, David; McIlduff, Courtney; Twydell, Paul; Young, Eufrosina; Johnson, Kristin; Rezania, Kourosh; Goyal, Namita A; Cohen, Jeffrey A; Benatar, Michael; Jones, Vovanti; Glass, Jonathan; Shah, Jaimin; Beydoun, Said R; Wymer, James P; Zilliox, Lindsay; Nayar, Shakti; Pattee, Gary L; Martinez-Thompson, Jennifer; Harvey, Brittany; Patel, Shital; Mahoney, Paul; Duda, Petra W; Cudkowicz, Merit E

Inhibiting 15-PGDH blocks blood-brain barrier deterioration and protects mice from Alzheimer's disease and traumatic brain injury

抑制15-PGDH可阻止血脑屏障的破坏,并保护小鼠免受阿尔茨海默病和创伤性脑损伤。

Koh, Yeojung; Vázquez-Rosa, Edwin; Gao, Farrah; Li, Hongyun; Chakraborty, Suwarna; Tripathi, Sunil Jamuna; Barker, Sarah; Bud, Zea; Bangalore, Anusha; Kandjoze, Uapingena P; León-Alvarado, Rose A; Sridharan, Preethy S; Cordova, Brittany A; Yu, Youngmin; Hyung, Jiwon; Fang, Hua; Singh, Salendra; Katabathula, Ramachandra; LaFramboise, Thomas; Kasturi, Lakshmi; Lutterbaugh, James; Beard, Lydia; Cordova, Erika; Cintrón-Pérez, Coral J; Franke, Kathryn; Fragoso, Mariana Franco; Miller, Emiko; Indrakumar, Vidya; Noel, Kamryn L; Dhar, Matasha; Ajroud, Kaouther; Zamudio, Carlos; Lopes, Filipa Blasco Tavares Pereira; Bambakidis, Evangeline; Zhu, Xiongwei; Wilson, Brigid; Flanagan, Margaret E; Gefen, Tamar; Fujioka, Hisashi; Fink, Stephen P; Desai, Amar B; Dawson, Dawn; Williams, Noelle S; Kim, Young-Kwang; Ready, Joseph M; Paul, Bindu D; Shin, Min-Kyoo; Markowitz, Sanford D; Pieper, Andrew A

The Impact of Diabetes and Metabolic Syndrome Burden on Pain, Neuropathy Severity and Fiber Type

糖尿病和代谢综合征负担对疼痛、神经病变严重程度和纤维类型的影响

Davalos, Long; Callaghan, Brian C; Muthukumar, Lavanya; Thomas, Simone; Reynolds, Evan L; Smith, A Gordon; Singleton, J Robinson; Höke, Ahmet; Ajroud-Driss, Senda; Dimachkie, Mazen M; Geisler, Stefanie; Simpson, David M; Stino, Amro M

Multicenter Expanded Access Protocol for Research Through Access to Trehalose in People With Amyotrophic Lateral Sclerosis

通过获取海藻糖,为肌萎缩侧索硬化症患者开展研究的多中心扩大使用方案

Krivickas, Brooke; Scirocco, Erica; Giacomelli, Elisa; Sharma, Saloni; Benson, Molly; Keegan, Mackenzie; Kulesa-Kelley, Jennifer; Chibnik, Lori B; Casagrande, Gabriella; Heyd, Lindsay; Chase, Marianne; Drake, Kristin; Mohapatra, Silpa; Hagar, Jennifer Linn; Hasenoehrl, Meredith Gibbons; Dagostino, Derek; Sherman, Alexander V; Leite, Alex; Yu, Hong; Rosenthal, Jesse; Miller, Timothy; McCaffrey, Alexandra; Gwathmey, Kelly; Locatelli, Eduardo; Bayat, Elham; Heitzman, Daragh; Young, Eufrosina; Goyal, Namita A; Whitesell, Jackie; Felice, Kevin; Ilieva, Hristelina; Swenson, Andrea; Walk, David; Alameda, Gustavo; Foster, Laura; McIlduff, Courtney E; Walsh, Alison; Zilliox, Lindsay; Ajroud-Driss, Senda; Bodkin, Cynthia; Katz, Jonathan; Ladha, Shafeeq; Rivner, Michael; Rosow, Laura; Twydell, Paul; Wasiewski, Warren; Babu, Suma; Berry, James D; Paganoni, Sabrina

Cytoplasmic expression of trans-active response DNA-binding protein-43 in aged mice display hippocampal sclerosis-like degeneration and neuronal loss with reduced lifespan.

老年小鼠胞质中反式活性反应DNA结合蛋白-43的表达表现为海马硬化样退化和神经元丢失,并伴有寿命缩短

Anderson Ashley J, Dopler Matthew B, Arezoumandan Sanaz, Osei-Kankam Damian, Davis Stephani A, Ajroud Kaouther, Lilek Jaclyn, Bambakadis Eva, Shapiro Rachel, Flanagan Margaret E, Cairns Nigel J, Gitcho Michael A