日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Predicting trajectories of the north star ambulatory assessment total score in Duchenne muscular dystrophy

预测杜氏肌营养不良症患者北极星步行评估总分的轨迹

Muntoni, Francesco; Signorovitch, James; Goemans, Nathalie; Manzur, Adnan Y; Done, Nicolae; Sajeev, Gautam; Li, Jiayang; Akbarnejad, Hanane; Sharma, Aarushi; Ward, Susan J; Niks, Erik H; Servais, Laurant; Mercuri, Eugenio; Guglieri, Michela; Straub, Volker; de Groot, Imelda; Ridout, Deborah; McDonald, Craig

Potential Utility of C-reactive Protein for Tuberculosis Risk Stratification Among Patients With Non-Meningitic Symptoms at HIV Diagnosis in Low- and Middle-income Countries.

C反应蛋白在低收入和中等收入国家HIV诊断时出现非脑膜炎症状的患者结核病风险分层中的潜在应用价值

Dupnik Kathryn, Rivera Vanessa R, Dorvil Nancy, Duffus Yanique, Akbarnejad Hanane, Gao Yipeng, Liu Jingyi, Apollon Alexandra, Dumont Emelyne, Riviere Cynthia, Severe Patrice, Lavoile Kerlyne, Duran Mendicuti Maria Alejandra, Pierre Samuel, Rouzier Vanessa, Walsh Kathleen F, Byrne Anthony L, Joseph Patrice, Cremieux Pierre-Yves, Pape Jean William, Koenig Serena P

Patient and Caregiver Outcomes After Onasemnogene Abeparvovec Treatment: Findings from the Cure SMA 2021 Membership Survey

Onasemnogene Abeparvovec 治疗后患者及照护者结局:来自 2021 年 Cure SMA 会员调查的结果

Toro, Walter; Yang, Min; Georgieva, Mihaela; Anderson, Annika; LaMarca, Nicole; Patel, Anish; Akbarnejad, Hanane; Dabbous, Omar