日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Development of VNX-101, an adeno-associated virus with less immunogenicity and efficient long-term expression of a CD19 T cell engager

VNX-101 是一种腺相关病毒,其免疫原性较低,且能有效长期表达 CD19 T 细胞衔接器。

Currier, Mark A; Reha, Allen; Hutzen, Brian; Wang, Pin-Yi; Chen, Chun-Yu; Glaspell, Andrea M; Paudel, Siddhi Nath; Venkataramany, Akila S; Das, Debashree; Hanlon, Danielle; Kaspar, Allan; Varma, Samit; Kaspar, Brian; Morales, Pablo; Ralph, Peter; Johnson, Tonny; Weiss, Tania L; Cripe, Timothy P

Progress in sarcomas: Highlights from the 2023 annual meetingof the Connective Tissue Oncology Society

肉瘤研究进展:2023年结缔组织肿瘤学会年会亮点

Cripe, Timothy P; Roberts, Ryan D; Chandler, Dawn S; Setty, Bhuvana A; Chen, Sonja; Shenoy, Archana; Venkataramany, Akila S; Ringwalt, Emily M; Scharschmidt, Thomas; Utset-Ward, Thomas; Konieczkowski, David J; Grignol, Valerie P; Beane, Joel D; Ruff, Samantha M; Pollock, Raphael E

Employing splice-switching oligonucleotides and AAVrh74.U7 snRNA to target insulin receptor splicing and cancer hallmarks in osteosarcoma

利用剪接转换寡核苷酸和AAVrh74.U7 snRNA靶向骨肉瘤中的胰岛素受体剪接和癌症标志

Safiya Khurshid ,Akila S Venkataramany ,Matias Montes ,John F Kipp ,Ryan D Roberts ,Nicolas Wein ,Frank Rigo ,Pin-Yi Wang ,Timothy P Cripe ,Dawn S Chandler

Leveraging gene therapy to achieve long-term continuous or controllable expression of biotherapeutics

利用基因疗法实现生物治疗药物的长期持续或可控表达

Timothy P Cripe,Brian Hutzen,Mark A Currier,Chun-Yu Chen,Andrea M Glaspell,Grace C Sullivan,Julia M Hurley,Mackenzie R Deighen,Akila S Venkataramany,Xiaokui Mo,Joseph R Stanek,Anthony R Miller,Saranga Wijeratne,Vincent Magrini,Elaine R Mardis,Jerry R Mendell,Dawn S Chandler,Pin-Yi Wang

Heat increases full-length SMN splicing: promise for splice-augmenting therapies for SMA

热能促进全长SMN蛋白的剪接:有望为脊髓性肌萎缩症的剪接增强疗法带来希望

Dominguez, Catherine E; Cunningham, David; Venkataramany, Akila S; Chandler, Dawn S