Real-world evidence of Nusinersen treatment for patients with spinal muscular atrophy in the Kingdom of Saudi Arabia: Initial insights from the Saudi national spinal muscular atrophy program
沙特阿拉伯王国脊髓性肌萎缩症患者使用诺西那生治疗的真实世界证据:来自沙特国家脊髓性肌萎缩症项目的初步见解
期刊:Saudi Medical Journal
影响因子:1.5
doi:10.15537/smj.2025.46.12.20250107
Al-Jedai, Ahmed H; Almudaiheem, Hajer Yousef; Alaama, Tareef Y; Alsaman, Abdulaziz Saeed Saeid; Abdo Bashiri, Fahad; Almuhaizae, Mohammed Abdelrahman; Alghamdi, Fouad Abdullah; Alsakran, Aljohara A; Matter, Eman Ahmed Yousef; Ibrahim, Fahad Zuriqan