日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Implications of the FDA's new plausible mechanism framework for the development of a personalized in vivo prime editing platform

FDA新的合理机制框架对开发个性化体内先导基因编辑平台的影响

Feierman, Emily R; Whittaker, Madelynn N; Quigley, Aidan; Brooks, Dominique L; McVeigh, Paige; Nan, Angela X; Hsu, Alvin; Said, Hooda; Soliman, Ousamah Younoss; Giovenco, Ryan; Davidson, Beverly L; Alameh, Mohamad-Gabriel; Liu, David R; Wang, Xiao; Musunuru, Kiran; Ahrens-Nicklas, Rebecca C

SPARC: a structural pathogenicity algorithm for risk classification of hERG variants

SPARC:一种用于hERG变异风险分类的结构致病性算法

Chatelain, Frank C; de Oliveira, Barbara Ribeiro; Grataloup, Guillaume; Robert, Noé; Alameh, Malak; Thollet, Aurélie; Montnach, Jérôme; Feliciangeli, Sylvain; Rio, Aline; Bibault, Floriane; Bichet, Delphine; Bignucolo, Olivier; Extramiana, Fabrice; Majumder, Rupamanjari; Schott, Jean-Jacques; Probst, Vincent; Denjoy, Isabelle; Lesage, Florian; Loussouarn, Gildas; De Waard, Michel

Investigating the impact of hypoxia and syncytialization on lipid nanoparticle-mediated mRNA delivery to placental cells

研究缺氧和合胞体化对脂质纳米颗粒介导的mRNA向胎盘细胞递送的影响

Young, Rachel E; Vijayakumar, Tara; Reilley, Logan J; Darji, Krisha; Patel, Diya; Hofbauer, Samuel; Alameh, Mohamad-Gabriel; Weissman, Drew; Riley, Rachel

Bringing Pandemic Science to the Classroom: Building Public Health Capacity at a Rural Kentucky High School

将疫情科学引入课堂:在肯塔基州一所乡村高中建立公共卫生能力

Alameh, Sahar; Hoover, Anna G; Keck, James W; Berry, Scott M; Goodpaster, Sagan; Tucker, Savannah; Goodin, Ashley

Correction of a recurrent pathogenic variant in methylmalonic acidemia using adenine base editing

利用腺嘌呤碱基编辑技术纠正甲基丙二酸血症中的复发性致病变异

Kahn, Elena M; Said, Hooda; Qu, Ping; Alameh, Mohamad-Gabriel; Wang, Xiao; Musunuru, Kiran; Ahrens-Nicklas, Rebecca C

Evaluation of an H5 influenza virus mRNA-lipid nanoparticle (LNP) vaccine in lactating dairy cows

在泌乳奶牛中评估H5流感病毒mRNA-脂质纳米颗粒(LNP)疫苗

Santos, Jefferson J S; Souza, Carine K; Zanella, Giovana C; Goulart, Débora B; Arruda, Bailey; Boggiatto, Paola; Palmer, Mitchell V; Snyder, Celeste A; Kristula, Michaela A; Dickens, Charlene; Webb, Terry L; Atkinson, Reilly K; Dadonaite, Bernadeta; Dwivedi, Garima; Alameh, Mohamad-Gabriel; Bloom, Jesse D; Weissman, Drew; Althouse, Gary C; Baker, Amy L; Hensley, Scott E

Generation and characterization of a novel MHC-II tetramer for tracking and characterization of toxin B-specific CD4(+) T cell responses

生成并表征一种新型MHC-II四聚体,用于追踪和表征毒素B特异性CD4(+) T细胞反应

Maslanka, Jeffrey R; She, Qianxuan; Krauss, Kathleen S; Konopka, Emily N; Bayard, Nile U; Londregan, Jennifer; Alameh, Mohamad-Gabriel; Eisenlohr, Laurence C; Kutzler, Michele A; Zackular, Joseph P; Abt, Michael C

Seemingly Reverse Wenckebach Phenomenon, Truly Inverse Decremental Conduction

看似反向的文克巴赫现象,实则为反向递减传导

Olleik, Farah; Alameh, Ibrahim; Liu, Tong

Atrial Fibrillation in Athletes: Mechanisms, Management, and Future Directions

运动员心房颤动:机制、治疗及未来方向

Alameh, Ibrahim; Al Fout, Ghina; Ezekowitz, Michael D; Kamareddine, Mohammed

Patient-Specific In Vivo Gene Editing to Treat a Rare Genetic Disease

利用患者特异性体内基因编辑技术治疗罕见遗传疾病

Musunuru, Kiran; Grandinette, Sarah A; Wang, Xiao; Hudson, Taylor R; Briseno, Kevin; Berry, Anne Marie; Hacker, Julia L; Hsu, Alvin; Silverstein, Rachel A; Hille, Logan T; Ogul, Aysel N; Robinson-Garvin, Nancy A; Small, Juliana C; McCague, Sarah; Burke, Samantha M; Wright, Christina M; Bick, Sarah; Indurthi, Venkata; Sharma, Shweta; Jepperson, Michael; Vakulskas, Christopher A; Collingwood, Michael; Keogh, Katie; Jacobi, Ashley; Sturgeon, Morgan; Brommel, Christian; Schmaljohn, Ellen; Kurgan, Gavin; Osborne, Thomas; Zhang, He; Kinney, Kyle; Rettig, Garrett; Barbosa, Christopher J; Semple, Sean C; Tam, Ying K; Lutz, Cathleen; George, Lindsey A; Kleinstiver, Benjamin P; Liu, David R; Ng, Kim; Kassim, Sadik H; Giannikopoulos, Petros; Alameh, Mohamad-Gabriel; Urnov, Fyodor D; Ahrens-Nicklas, Rebecca C