日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Lafora disease gene therapy: EPM2A but not EPM2B overexpression results in Lafora body formation.

Lafora病基因治疗:EPM2A而非EPM2B过度表达会导致Lafora小体的形成。

Alao Esther O, Sheibani Mehrnaz, Wu Jun, Marriam Ummay, Evans Doretha, Kasiri Sahba, Verma Mayank, Nitschke Silvia, Nitschke Felix, Gray Steven J, Mitra Sharmistha, Minassian Berge A

Focused ultrasound widely broadens AAV-delivered Cas9 distribution and activity.

聚焦超声可显著扩大 AAV 递送的 Cas9 的分布和活性

Gumusgoz Emrah, Kasiri Sahba, Youssef Ibrahim, Verma Mayank, Chopra Rajiv, Villarreal Acha Daniel, Wu Jun, Marriam Ummay, Alao Esther, Chen Xin, Guisso Dikran R, Gray Steven J, Shah Bhavya R, Minassian Berge A