Clinical description and evaluation of 30 pediatric patients with ultra-rare diseases: A multicenter study with real-world data from Saudi Arabia
对30例患有超罕见疾病的儿科患者进行临床描述和评估:一项来自沙特阿拉伯的多中心真实世界数据研究
期刊:PLoS One
影响因子:2.6
doi:10.1371/journal.pone.0307454
Muthaffar, Osama Y; Alazhary, Noura W; Alyazidi, Anas S; Alsubaie, Mohammed A; Bahowarth, Sarah Y; Odeh, Nour B; Bamaga, Ahmed K