CRISPR/Cas9-edited PKP2 knock-out (JMUi001-A-2) and DSG2 knock-out (JMUi001-A-3) iPSC lines as an isogenic human model system for arrhythmogenic cardiomyopathy (ACM)
CRISPR/Cas9 编辑的 PKP2 敲除 (JMUi001-A-2) 和 DSG2 敲除 (JMUi001-A-3) iPSC 系作为心律失常性心肌病 (ACM) 的同源人类模型系统
期刊:Stem Cell Research
影响因子:0.8
doi:10.1016/j.scr.2021.102256
Anna Janz, Miriam Zink, Alexandra Cirnu, Annika Hartleb, Christina Albrecht, Simone Rost, Eva Klopocki, Katharina Günther, Frank Edenhofer, Süleyman Ergün, Brenda Gerull