Key measurement concepts and appropriate clinical outcome assessments in pediatric achondroplasia clinical trials
儿童软骨发育不全临床试验中的关键测量概念和适当的临床结果评估
期刊:Orphanet Journal of Rare Diseases
影响因子:3.5
doi:10.1186/s13023-022-02333-6
Aldhouse, Natalie V J; Kitchen, Helen; Johnson, Chloe; Marshall, Chris; Pegram, Hannah; Pease, Sheryl; Collins, Sam; Baker, Christine L; Beaverson, Katherine; Crews, Chandler; Massey, Jill; Wyrwich, Kathleen W