Applying genome-wide CRISPR-Cas9 screens for therapeutic discovery in facioscapulohumeral muscular dystrophy
应用全基因组 CRISPR-Cas9 筛选来发现面肩肱型肌营养不良症的治疗方法
期刊:Science Translational Medicine
影响因子:15.8
doi:10.1126/scitranslmed.aay0271
Angela Lek, Yuanfan Zhang, Keryn G Woodman, Shushu Huang, Alec M DeSimone, Justin Cohen, Vincent Ho, James Conner, Lillian Mead, Andrew Kodani, Anna Pakula, Neville Sanjana, Oliver D King, Peter L Jones, Kathryn R Wagner, Monkol Lek, Louis M Kunkel5
