Systemic γ-sarcoglycan AAV gene transfer results in dose-dependent correction of muscle deficits in the LGMD 2C/R5 mouse model
系统性 γ-肌聚糖 AAV 基因转移可导致 LGMD 2C/R5 小鼠模型中肌肉缺陷的剂量依赖性纠正
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:
doi:10.1016/j.omtm.2023.01.004
Young-Eun Seo, Stephen H Baine, Amber N Kempton, Oliver C Rogers, Sarah Lewis, Kaitlin Adegboye, Alex Haile, Danielle A Griffin, Ellyn L Peterson, Eric R Pozsgai, Rachael A Potter, Louise R Rodino-Klapac
