日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Systematic evaluation of AML-associated antigens identifies anti-U5 SNRNP200 therapeutic antibodies for the treatment of acute myeloid leukemia

对 AML 相关抗原的系统评估确定了用于治疗急性髓系白血病的抗 U5 SNRNP200 治疗性抗体

Katherine Knorr, Jahan Rahman, Caroline Erickson, Eric Wang, Mara Monetti, Zhuoning Li, Juliana Ortiz-Pacheco, Andrew Jones, Sydney X Lu, Robert F Stanley, Maria Baez, Nina Fox, Cynthia Castro, Alessandra E Marino, Caroline Jiang, Alex Penson, Simon J Hogg, Xiaoli Mi, Hideaki Nakajima, Hiroyoshi Kun

Aberrant EVI1 splicing contributes to EVI1-rearranged leukemia

异常 EVI1 剪接导致 EVI1 重排白血病

Atsushi Tanaka, Taizo A Nakano, Masaki Nomura, Hiromi Yamazaki, Jan P Bewersdorf, Roger Mulet-Lazaro, Simon Hogg, Bo Liu, Alex Penson, Akihiko Yokoyama, Weijia Zang, Marije Havermans, Miho Koizumi, Yasutaka Hayashi, Hana Cho, Akinori Kanai, Stanley C Lee, Muran Xiao, Yui Koike, Yifan Zhang, Miki Fuk

SF3B1 mutant-induced missplicing of MAP3K7 causes anemia in myelodysplastic syndromes

SF3B1 突变诱导的 MAP3K7 错误剪接导致骨髓增生异常综合征患者出现贫血

Yen K Lieu, Zhaoqi Liu, Abdullah M Ali, Xin Wei, Alex Penson, Jian Zhang, Xiuli An, Raul Rabadan, Azra Raza, James L Manley, Siddhartha Mukherjee1

Minor intron retention drives clonal hematopoietic disorders and diverse cancer predisposition

次要内含子保留驱动克隆性造血疾病和多种癌症易感性

Daichi Inoue # ,Jacob T Polaski # ,Justin Taylor # ,Pau Castel ,Sisi Chen ,Susumu Kobayashi ,Simon J Hogg ,Yasutaka Hayashi ,Jose Mario Bello Pineda ,Ettaib El Marabti ,Caroline Erickson ,Katherine Knorr ,Miki Fukumoto ,Hiromi Yamazaki ,Atsushi Tanaka ,Chie Fukui ,Sydney X Lu ,Benjamin H Durham ,Bo Liu ,Eric Wang ,Sanjoy Mehta ,Daniel Zakheim ,Ralph Garippa ,Alex Penson ,Guo-Liang Chew ,Frank McCormick ,Robert K Bradley ,Omar Abdel-Wahab

Altered RNA Splicing by Mutant p53 Activates Oncogenic RAS Signaling in Pancreatic Cancer

突变 p53 改变的 RNA 剪接激活胰腺癌中的致癌 RAS 信号传导

Luisa F Escobar-Hoyos, Alex Penson, Ram Kannan, Hana Cho, Chun-Hao Pan, Rohit K Singh, Lisa H Apken, G Aaron Hobbs, Renhe Luo, Nicolas Lecomte, Sruthi Babu, Fong Cheng Pan, Direna Alonso-Curbelo, John P Morris 4th, Gokce Askan, Olivera Grbovic-Huezo, Paul Ogrodowski, Jonathan Bermeo, Joseph Saglimbe

Modeling biological and genetic diversity in upper tract urothelial carcinoma with patient derived xenografts

利用患者来源的异种移植模型建立上尿路上皮癌的生物和遗传多样性

Kwanghee Kim #, Wenhuo Hu #, François Audenet, Nima Almassi, Aphrothiti J Hanrahan, Katie Murray, Aditya Bagrodia, Nathan Wong, Timothy N Clinton, Shawn Dason, Vishnu Mohan, Sylvia Jebiwott, Karan Nagar, Jianjiong Gao, Alex Penson, Chris Hughes, Benjamin Gordon, Ziyu Chen, Yiyu Dong, Philip A Watson

Spliceosomal disruption of the non-canonical BAF complex in cancer

癌症中非经典 BAF 复合物的剪接体破坏

Daichi Inoue #, Guo-Liang Chew #, Bo Liu, Brittany C Michel, Joseph Pangallo, Andrew R D'Avino, Tyler Hitchman, Khrystyna North, Stanley Chun-Wei Lee, Lillian Bitner, Ariele Block, Amanda R Moore, Akihide Yoshimi, Luisa Escobar-Hoyos, Hana Cho, Alex Penson, Sydney X Lu, Justin Taylor, Yu Chen, Cigal

Therapeutic Targeting of RNA Splicing Catalysis through Inhibition of Protein Arginine Methylation

通过抑制蛋白质精氨酸甲基化来靶向RNA剪接催化进行治疗

Jia Yi Fong,Luca Pignata,Pierre-Alexis Goy,Kimihito Cojin Kawabata,Stanley Chun-Wei Lee,Cheryl M Koh,Daniele Musiani,Enrico Massignani,Andriana G Kotini,Alex Penson,Cheng Mun Wun,Yudao Shen,Megan Schwarz,Diana Hp Low,Alexander Rialdi,Michelle Ki,Heike Wollmann,Slim Mzoughi,Florence Gay,Christine Thompson,Timothy Hart,Olena Barbash,Genna M Luciani,Magdalena M Szewczyk,Bas J Wouters,Ruud Delwel,Eirini P Papapetrou,Dalia Barsyte-Lovejoy,Cheryl H Arrowsmith,Mark D Minden,Jian Jin,Ari Melnick,Tiziana Bonaldi,Omar Abdel-Wahab,Ernesto Guccione

Mutational landscape, clonal evolution patterns, and role of RAS mutations in relapsed acute lymphoblastic leukemia

复发性急性淋巴细胞白血病中的突变景观、克隆进化模式和 RAS 突变的作用

Koichi Oshima, Hossein Khiabanian, Ana C da Silva-Almeida, Gannie Tzoneva, Francesco Abate, Alberto Ambesi-Impiombato, Marta Sanchez-Martin, Zachary Carpenter, Alex Penson, Arianne Perez-Garcia, Cornelia Eckert, Concepción Nicolas, Milagros Balbin, Maria Luisa Sulis, Motohiro Kato, Katsuyoshi Koh, M

Disease-associated mutation in SRSF2 misregulates splicing by altering RNA-binding affinities

SRSF2 中的疾病相关突变通过改变 RNA 结合亲和力错误调节剪接

Jian Zhang, Yen K Lieu, Abdullah M Ali, Alex Penson, Kathryn S Reggio, Raul Rabadan, Azra Raza, Siddhartha Mukherjee, James L Manley