Lipid-siRNA conjugate accesses perivascular transport and achieves durable knockdown throughout the central nervous system
脂质-siRNA 结合物可进入血管周围运输并在整个中枢神经系统中实现持久敲低
期刊:
影响因子:
doi:10.1101/2024.06.09.598079
Alexander G Sorets, Katrina R Schwensen, Nora Francini, Andrew Kjar, Adam M Abdulrahman, Alena Shostak, Ketaki A Katdare, Kathleen M Schoch, Rebecca P Cowell, Joshua C Park, Alexander P Ligocki, William T Ford, Lissa Ventura-Antunes, Ella N Hoogenboezem, Alex Prusky, Mark Castleberry, Danielle L Mic