Cellular Modeling of CLN6 with IPSC-derived Neurons and Glia
使用 IPSC 衍生的神经元和神经胶质细胞对 CLN6 进行细胞建模
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doi:10.1101/2024.01.29.577876
Maria Gabriela Otero, Jaemin Kim, Yogesh Kumar Kushwaha, Alex Rajewski, Fabian David Nonis, Chintda Santiskulvong, Serguei I Bannykh, Hiral Oza, Hafiz Muhammad Umer Farooqi, Madeline Babros, Christina Freeman, Lucie Dupuis, Saadat Mercimek-Andrews, Roberto Mendoza-Londono, Catherine Bresee, David R