Evaluator Training and Reliability for SMA Global Nusinersen Trials1
SMA 全球 Nusinersen 试验的评估者培训和可靠性1
期刊:Journal of Neuromuscular Diseases
影响因子:3.4
doi:10.3233/JND-180301
Glanzman, Allan M; Mazzone, Elena S; Young, Sally Dunaway; Gee, Richard; Rose, Kristy; Mayhew, Anna; Nelson, Leslie; Yun, Chris; Alexander, Katie; Darras, Basil T; Zolkipli-Cunningham, Zarazuela; Tennekoon, Gihan; Day, John W; Finkel, Richard S; Mercuri, Eugenio; De Vivo, Darryl C; Baldwin, Ron; Bishop, Kathie M; Montes, Jacqueline