Allosteric Modulation of Pathological Ataxin-3 Aggregation: A Path to Spinocerebellar Ataxia Type-3 Therapies
病理性共济失调蛋白 3 聚集的变构调节:脊髓小脑共济失调 3 型治疗的途径
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doi:10.1101/2025.01.22.633970
Alexandra Silva, Sara Duarte-Silva, Pedro M Martins, Beatriz Rodrigues, Débora Serrenho, Daniela Vilasboas-Campos, Andreia Teixeira-Castro, Julio Vieyto-Nuñez, Joel Mieres-Perez, Francisco Figueiredo, Joana Fraga, James Noble, Carter Lantz, Niki Sepanj, Daniela Monteiro-Fernandes, Sara Guerreiro, An