Lipid nanoparticle delivery limits antisense oligonucleotide activity and cellular distribution in the brain after intracerebroventricular injection
脂质纳米颗粒递送限制脑室内注射后反义寡核苷酸的活性和脑细胞分布
期刊:Molecular Therapy-Nucleic Acids
影响因子:6.5
doi:10.1016/j.omtn.2023.05.005
Amy E Byrnes, Sara L Dominguez, Chun-Wan Yen, Benjamin I Laufer, Oded Foreman, Mike Reichelt, Han Lin, Meredith Sagolla, Kathy Hötzel, Hai Ngu, Christoffer Soendergaard, Alberto Estevez, Hsiu-Chao Lin, Alexandre Goyon, Juan Bian, Jessica Lin, Flora I Hinz, Brad A Friedman, Amy Easton, Casper C Hooge