日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Elexacaftor/Tezacaftor/Ivacaftor for Cystic Fibrosis and Rare CFTR Variants: In Vitro Translation to a Phase 3, Double-Blind, Randomized, Placebo-controlled Trial and Real-World Study

Elexacaftor/Tezacaftor/Ivacaftor 用于囊性纤维化和罕见 CFTR 变异:体外研究向 3 期双盲、随机、安慰剂对照试验和真实世界研究的转化

Castellani, Carlo; Mondejar-Lopez, Pedro; Van Goor, Fredrick; Quon, Bradley S; Alghisi, Federico; Fabrizzi, Benedetta; Ramsey, Bonnie; Taylor-Cousar, Jennifer L; McKone, Edward F; Tullis, Elizabeth; Weinstock, Tanya G; Tan, Vincent; Ahluwalia, Neil; Mahic, Milada; Liu, Lingyun; Saayman, Sheena; Altshuler, David; Waltz, David; Mall, Marcus A; Fajac, Isabelle

Phosphatidylserine liposomes for Mycobacterium abscessus infections management in people with cystic fibrosis non-eligible for CFTR modulators

磷脂酰丝氨酸脂质体用于治疗不适合使用 CFTR 调节剂的囊性纤维化患者的脓肿分枝杆菌感染

Olimpieri, Tommaso; Poerio, Noemi; Saliu, Fabio; Lorè, Nicola I; Ciciriello, Fabiana; Ponsecchi, Greta; Alghisi, Federico; Cirillo, Daniela M; D'Andrea, Marco M; Fraziano, Maurizio

Prenatal Elexacaftor/Tezacaftor/Ivacaftor for Fetal Meconium Ileus: First Italian Case and Narrative Overview of the Emerging Evidence

产前使用Elexacaftor/Tezacaftor/Ivacaftor治疗胎儿胎粪性肠梗阻:首例意大利病例及新兴证据概述

Boni, Alessandra; Vassallo, Chiara; Ciciriello, Fabiana; Cristiani, Luca; Mancini, Alessandro; Zucaro, Luigi; Graziano, Sonia; Goffredo, Bianca Maria; Alghisi, Federico; Raponi, Massimiliano; Fabietti, Isabella; On Behalf Of Opbg Cf Pregnancy And Fetal Therapy Multidisciplinary Group

Development and Validation of a New LC-MS/MS Method for Simultaneous Quantification of Ivacaftor, Tezacaftor and Elexacaftor Plasma Levels in Pediatric Cystic Fibrosis Patients

开发和验证一种新的LC-MS/MS方法,用于同时定量分析儿童囊性纤维化患者血浆中伊伐卡托、替扎卡托和依来卡托的浓度

Mancini, Alessandro; Simeoli, Raffaele; Cristiani, Luca; Cairoli, Sara; Ciciriello, Fabiana; Boni, Alessandra; Alghisi, Federico; Rossi, Chiara; Antonetti, Giacomo; Vici, Carlo Dionisi; Fiocchi, Alessandro Giovanni; Cutrera, Renato; Goffredo, Bianca Maria

Phosphatidylinositol 5-Phosphate-Loaded Apoptotic Body-Like Liposomes for Mycobacterium abscessus Infection Management in Patients With Cystic Fibrosis

用于囊性纤维化患者脓肿分枝杆菌感染治疗的磷脂酰肌醇5-磷酸负载凋亡小体样脂质体

Olimpieri, Tommaso; Poerio, Noemi; Saliu, Fabio; Lorè, Nicola I; Ciciriello, Fabiana; Ponsecchi, Greta; D'Andrea, Marco M; Alghisi, Federico; Cirillo, Daniela M; Fraziano, Maurizio

Height Velocity in Pediatric Cystic Fibrosis Under Triple CFTR Modulator Therapy: A Real-Life Monocentric Experience

三重CFTR调节剂治疗下儿童囊性纤维化身高增长速度:一项真实的单中心研究

Boni, Alessandra; d'Aniello, Francesco; Ubertini, Grazia; Cappa, Marco; Ciciriello, Fabiana; Majo, Fabio; Cristiani, Luca; Alghisi, Federico; Montemitro, Enza; Bella, Sergio; De Marchis, Matteo; Cutrera, Renato; Fiocchi, Alessandro G

Pancreatitis Preceding the Diagnosis of IBD in Children: A Retrospective Observational Study

儿童IBD诊断前发生的胰腺炎:一项回顾性观察研究

D'Antonio, Lorenzo; Balassone, Valerio; Alghisi, Federico; Imondi, Chiara; Rea, Francesca; Romeo, Erminia; Angelino, Giulia; Cardile, Sabrina; Knafelz, Daniela; Bracci, Fiammetta; De Angelis, Paola; Faraci, Simona

Distribution of OGTT-Related Variables in Patients with Cystic Fibrosis from Puberty to Adulthood: An Italian Multicenter Study

囊性纤维化患者从青春期到成年期口服葡萄糖耐量试验相关变量的分布:一项意大利多中心研究

Foppiani, Andrea; Ciciriello, Fabiana; Bisogno, Arianna; Bricchi, Silvia; Colombo, Carla; Alghisi, Federico; Lucidi, Vincenzina; Catena, Maria Ausilia; Lucanto, Mariacristina; Mari, Andrea; Bedogni, Giorgio; Battezzati, Alberto

An inflammatory Signature of Glucose Impairment in Cystic Fibrosis.

囊性纤维化中葡萄糖代谢障碍的炎症特征

Montemari Anna Lisa, Manco Melania, Fiocchi Alessandro Giovanni, Bartoli Manuela, Facchiano Francesco, Tabolacci Claudio, Scatigna Maria, Ciciriello Fabiana, Alghisi Federico, Montemitro Enza, Carsetti Rita, Lucidi Vincenzina, Fiscarelli Ersilia Vita

Clinical course and risk factors for severe COVID-19 among Italian patients with cystic fibrosis: a study within the Italian Cystic Fibrosis Society

意大利囊性纤维化患者罹患重症 COVID-19 的临床病程和危险因素:一项由意大利囊性纤维化协会开展的研究

Colombo, Carla; Cipolli, Marco; Daccò, Valeria; Medino, Paola; Alghisi, Federico; Ambroni, Maura; Badolato, Raffaele; Battistini, Fiorella; Bignamini, Elisabetta; Casciaro, Rosaria; Ciciriello, Fabiana; Collura, Mirella; Comello, Isabella; Francalanci, Michela; Ficili, Francesca; Folino, Anna; Leonardi, Salvatore; Leonetti, Giuseppina; Lucanto, Maria Cristina; Lucca, Francesca; Maschio, Massimo; Mencarini, Valeria; Messore, Barbara; Pisi, Giovanna; Pizzamiglio, Giovanna; Poli, Piercarlo; Raia, Valeria; Riberi, Luca; Ros, Mirco; Rotolo, Novella; Sepe, Angela; Taccetti, Giovanni; Vitullo, Pamela; Alicandro, Gianfranco