Signal Peptide Engineering and Codon Optimization to Enhance α-Gal A Activity for rAAV Gene Therapy of Fabry Disease
信号肽工程和密码子优化增强α-半乳糖苷酶A活性,用于法布里病的rAAV基因治疗
期刊:Journal of Inherited Metabolic Disease
影响因子:3.8
doi:10.1002/jimd.70168
He, Siwu; Yang, Li; Wan, Ke; Zheng, Zhaoyue; Leng, Mi; Gan, Chunmei; Liu, Yu; Xiao, Lin; Ye, Jingya; Chen, Zhian; Zhou, Jiao; Valencia, C Alexander; Abuammah, Aliah; Chow, Hoi Yee; Dong, Biao; Chen, Yucheng