日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

CD19 CAR-T cells for treatment-refractory autoimmune diseases: the phase 1/2 CASTLE basket trial

CD19 CAR-T 细胞治疗难治性自身免疫性疾病:CASTLE 篮子试验(1/2 期)

Müller, Fabian; Hagen, Melanie; Wirsching, Andreas; Kharboutli, Soraya; Aigner, Michael; Völkl, Simon; Kretschmann, Sascha; Tascilar, Koray; Taubmann, Jule; Bucci, Laura; Raimondo, Maria Gabriella; Bergmann, Christina; Rothe, Tobias; Corte, Giulia; Tur, Carlo; Muñoz, Luis; Böltz, Sebastian; Schuster, Louis; Hartmann, Fabian; Garantziotis, Panagiotis; Spörl, Silvia; Vasova, Ingrid; Gerbitz, Armin; Spriewald, Bernd; Kiener, Hans; Giannarelli, Diana; Locatelli, Franco; D'Agostino, Maria-Antonietta; Hanssens, Linda; Miltenyi, Stefan; Bozec, Aline; Grieshaber-Bouyer, Ricardo; Mackensen, Andreas; Schett, Georg

Butyrolactol A enhances caspofungin efficacy via flippase inhibition in drug-resistant fungi.

丁内酯 A 通过抑制抗药真菌中的翻转酶来增强卡泊芬净的疗效。

Chen Xuefei, Duan H Diessel, Hoy Michael J, Koteva Kalinka, Spitzer Michaela, Guitor Allison K, Puumala Emily, Fiebig Aline A, Hu Guanggan, Yiu Bonnie, Chou Sommer, Bian Zhuyun, Choi Yeseul, Guo Amelia Bing Ya, Wang Wenliang, Sun Sheng, Robbins Nicole, Averette Anna Floyd, Cook Michael A, Truant Ray, MacNeil Lesley T, Brown Eric D, Kronstad James W, Coombes Brian K, Cowen Leah E, Heitman Joseph, Li Huilin, Wright Gerard D

Systematic analysis of snRNA genes reveals frequent RNU2-2 variants in dominant and recessive developmental and epileptic encephalopathies

对snRNA基因的系统分析揭示了显性和隐性发育性脑病和癫痫性脑病中常见的RNU2-2变异。

Leitão, Elsa; Santini, Amandine; Cogne, Benjamin; Essid, Miriam; Athanasiadou, Maria; LaFlamme, Christy W; Marijon, Pierre; Bernard, Virginie; Jousselin, Kevin; Chatron, Nicolas; Barcia, Giulia; Keren, Boris; Mignot, Cyril; Charles, Perrine; Besnard, Thomas; Paluch, Robin; de Sainte Agathe, Jean-Madeleine; Almanza Fuerte, Edith P; Sengupta, Soham; Milh, Mathieu; Ramond, Francis; Allan, Talia; An, Isabelle; Araujo, Camila; Arpin, Stéphanie; Austin-Tse, Christina; Auvin, Stéphane; Baer, Sarah; Bahi-Buisson, Nadia; Bak, Mads; Barth, Magalie; Baulac, Stéphanie; Bednarek-Weirauch, Nathalie; Begemann, Matthias; Bennett, Mark F; Bensabath, Uriel; Bézieau, Stéphane; Bhouri, Rakia; Biehler, Margaux; Hammer, Trine Bjørg; Bogoin, Julie; Bonanno, Emilie; Boussion, Simon; Bris, Céline; Brosseau-Beauvir, Adelaide; Bruel, Ange-Line; Briand-Suleau, Audrey; Buratti, Julien; Celse, Tristan; Chambon, Pascal; Chemaly, Nicole; Chesneau, Bertrand; Colin, Estelle; Colmard, Maxime; Colson, Cindy; Conrad, Solène; Courtin, Thomas; Creveaux, Isabelle; Cullier, Anne-Charlotte; Dang, Louis T; de Saint Martin, Anne; de Vanssay de Blavous Legendre, Caroline; Demeer, Bénédicte; Denommé-Pichon, Anne-Sophie; Diekhoff, Philine; DiTroia, Stephanie; Doco-Fenzy, Martine; Dubourg, Christèle; Dubucs, Charlotte; Ducreux, Stéphanie; Dufour, Louis; Duquet, Romain; Durand, Benjamin; El Chehadeh, Salima; Elbracht, Miriam; Faivre, Laurence; Faoucher, Marie; Faudet, Anne; Forlani, Sylvie; Fradin, Mélanie; Gaignard, Pauline; Ganne, Benjamin; Garde, Aurore; Géraud, Justine; Gill, Deepak; Goldenberg, Alice; Grabli, David; Grisel, Coraline; Gueden, Sophie; Gueguen, Paul; Guerrot, Anne-Marie; Guichet, Agnès; Haack, Tobias B; Härting, Nina; Häusler, Martin Georg; Heide, Solveig; Herget, Theresia; Héron, Bénédicte; Héron, Delphine; Herwig, Johanna; Heulin, Mathilde; Holling, Tess; Houdayer, Clara; Isidor, Bertrand; Jacquette, Aurélia; Januel, Louis; Jean-Marçais, Nolwenn; Kaiser, Frank J; Kaya, Sabine; King, Chontelle; Konyukh, Marina; Kraft, Florian; Krause, Jeremias; Kirstetter, Rémi; Kuechler, Alma; Kurth, Ingo; Kutsche, Kerstin; Labalme, Audrey; Laloy, Jean-Serene; Laugel, Vincent; Le Bricquir, Floriane; Lèbre, Anne-Sophie; Lebrun, Marine; Leguern, Eric; Levy, Jonathan; Lieffering, Nico; Lyonnet, Stanislas; Lüthy, Kevin; Macdonald, Sian M W; Mansour-Hendili, Lamisse; Maraval, Julien; Marquardt, Iris; Mattausch, Carolin; Mercier, Sandra; Messaoud, Olfa; Morel, Godelieve; Mortreux, Jérémie; Munnich, Arnold; Nabbout, Rima; Nambot, Sophie; Navarro, Vincent; Neale, Ashana; Nguyen, Laetitia; Nizon, Mathilde; Nowak, Frédérique; O'Leary, Melanie C; Odent, Sylvie; Ojeda, Naomi Meave; Olin, Valérie; Olivieri, Simone; Õunap, Katrin; Pais, Lynn S; Panagiotakaki, Eleni; Patat, Olivier; Perrin-Sabourin, Laurence; Petit, Florence; Philippe, Christophe; Piton, Amélie; Planes, Marc; Poirsier, Céline; Pouzet, Antoine; Prouteau, Clément; Quéméner-Redon, Sylvia; Renaud, Mathilde; Richard, Anne-Claire; Rio, Marlène; Rivier, Clotilde; Robin-Renaldo, Florence; Rollier, Paul; Rossi, Massimiliano; Roubertie, Agathe; Ruault, Valentin; Rupin-Mas, Maïlys; Saugier-Veber, Pascale; Saunier, Aline; Saneto, Russell; Sarrazin, Elisabeth; Sarret, Catherine; Schaefer, Elise; Schluth-Bolard, Caroline; Schneider, Amy; Schumann, Isabell; Seplyarskiy, Vladimir B; Spranger, Stephanie; Smol, Thomas; Sturm, Marc; Sunyaev, Shamil R; Sperelakis-Beedham, Brian; Stenton, Sarah L; Stock, Friedrich; Tharreau, Mylène; Torun, Deniz; Toulouse, Joseph; Thiyagarajah, Harshini; Valence, Stéphanie; Valleix, Sophie; Van-Gils, Julien; Villard, Laurent; Ville, Dorothée; Villeneuve, Nathalie; Vitobello, Antonio; Waernessyckle, Aurélie; Wagner, Jan; Weber, Yvonne; Wieczorek, Dagmar; Witkowski, Tom; Yadavilli, Manya; Yammine, Tony; Zaafrane-Khachnaoui, Khaoula; Zaki, Maha S; Ziegler, Alban; Bramswig, Nuria C; Lermine, Alban; Nicolas, Gael; Gleeson, Joseph G; Sadleir, Lynette G; Hildebrand, Michael S; Scheffer, Ingrid E; Whiffin, Nicola; O'Donnell-Luria, Anne; Mefford, Heather C; Blanc, Pierre; Thevenon, Julien; Charbonnier, Camille; Charenton, Clément; Depienne, Christel; Lesca, Gaetan; Nava, Caroline

Prophylactic Treatment of Patent Ductus Arteriosus With Acetaminophen: A Randomized Clinical Trial

对乙酰氨基酚预防动脉导管未闭:一项随机临床试验

Rozé, Jean-Christophe; Cambonie, Gilles; Flamant, Cyril; Patkaï, Juliana; Mühlbacher, Tobias; Gascoin, Geraldine; Rideau Batista Novais, Aline; Tauzin, Manon; Le Duc, Kevin; Beuchée, Alain; Joye, Sebastien; Babacheva, Evgeniya; Bouissou, Antoine; Ligi, Isabelle; Tammela, Outi; Plourde, Marion; Dempsey, Eugene; Tosello, Barthelemy; Nguyen, Kim; Vincent, Marine; Andresson, Pille; Binder, Christoph; Kruse, Charlotte; Barcos Munoz, Francisca; Kuhn, Pierre; Proença, Elisa; Bartocci, Marco; Kermorvant-Duchemin, Elsa; Nellis, Georgi; Lumia, Mirka; Giapros, Vasileios; Rigo, Vincent; Sankilampi, Ulla; Mendes da Graça, André; Rønnestad, Arild; Soukka, Hanna; Mondì, Vito; Aikio, Outi; Torre-Monmany, Nuria; Rüegger, Christoph; Baud, Olivier; Zeitlin, Jennifer; Morgan, Andrei Scott; Baruteau, Alban-Elouen; Ancel, Pierre-Yves; Carbajal, Ricardo; Bouazza, Naim; Diallo, Alpha; Levoyer, Lea; Kemper, Ruth; Hallman, Mikko; Alberti, Corinne; Ursino, Moreno

Latent transition analysis for longitudinal studies of post-acute infection syndromes

潜在转换分析在急性感染后综合征纵向研究中的应用

Gusinow, Roy; Górska, Anna; Canziani, Lorenzo Maria; Lopes-Rafegas, Iris; Alvarez Garavito, Carolina; Tami, Adriana; Gentilotti, Elisa; Sicuri, Elisa; Laouénan, Cédric; Ghosn, Jade; Florence, Aline-Marie; Lahfej, Nadhem; Mazzaferri, Fulvia; Del Piccolo, Lidia; Giannella, Maddalena; Toschi, Alice; Di Chiara, Michela; Caponcello, Maria Giulia; Palacios-Baena, Zaira R; Wold, Karin I; Rossi, Elisa; Tacconelli, Evelina; Hasenauer, Jan

Lucerastat, an oral therapy for Fabry disease: results from a pivotal randomized phase 3 study and its open-label extension

Lucerastat,一种用于治疗法布里病的口服药物:一项关键性随机3期研究及其开放标签扩展研究的结果

Nordbeck, Peter; Goker-Alpan, Ozlem; Bernat, John A; Germain, Dominique P; Giraldo, Pilar; Jovanovic, Ana; Kimonis, Virginia; Nicholls, Kathleen; Rockman-Greenberg, Cheryl; Schiffmann, Raphael; Thomas, Mark; Tylki-Szymanska, Anna; Wallace, Eric; Welford, Richard W D; West, Michael L; Clozel, Martine; Frey, Aline; Trokan, Luba; Mueller, Markus S; Vogler, Markus; Wanner, Christoph; Hughes, Derralynn

Nivolumab in combination with AVD as frontline treatment for patients with classic Hodgkin lymphoma: A real‐world analysis from 20 US centers

纳武利尤单抗联合AVD方案作为经典型霍奇金淋巴瘤患者的一线治疗:来自美国20个中心的真实世界分析

Quinquenel, Anne; Aurran-Schleinitz, Thérèse; Clavert, Aline; Cymbalista, Florence; Dartigeas, Caroline; Davi, Frédéric; de Guibert, Sophie; Delmer, Alain; Dilhuydy, Marie-Sarah; Feugier, Pierre; Fornecker, Luc-Matthieu; Ghez, David; Guieze, Romain; Laribi, Kamel; Leblond, Véronique; Leprêtre, Stéphane; Letestu, Rémi; Lévy, Vincent; Nguyen-Khac, Florence; Michallet, Anne-Sophie; Tomowiak, Cécile; Tournilhac, Olivier; Ysebaert, Loïc; Troussard, Xavier; Bock, Allison M; Hao, Peirong; Xu, Yizhe; Luttwak, Efrat; Thiruvengadam, Swetha Kambhampati; Sekaran, Kanithra; Sano, Dahlia; Vaughn, John; Sharp, John; Major, Ajay; Patel, Vrutti; Smilnak, Gordon; Araujo, Nicole; Mynam, Ritwick; Reef, Daniel; Palmeri, Marisa; Gerber, Drew; Abhyankar, Anuja; Baek, Grace; Falade, Ayo; Iqbal, Madiha; Hu, Boyu; Geethakumari, Praveen Ramakrishnan; Durani, Urshila; Di, Mengyang; Niu, Alex; Cherng, Hua‐Jay J; Rhodes, Joanna M; Grover, Natalie; Pophali, Priyanka; Feldman, Tatyana; Shanmugasundaram, Krithika; Svoboda, Jakub; Voorhees, Timothy; Diefenbach, Catherine; Karimi, Yasmin; Karmali, Reem; Herrera, Alex F; Torka, Pallawi; Epperla, Narendranath

Unveiling the Formation and Evolution of the Cathode-Electrolyte Interphase in Lithium-Sulfur Batteries

揭示锂硫电池正极-电解质界面形成与演变

Machado Amaral, Murilo; Jovino Marques, Otavio; de Navarro de Miranda, André; Oliveira, Aline Carlos; Doubek, Gustavo; Singh, Gurpreet; Zanin, Hudson; Garcia Freitas, Renato; Nelson Weker, Johanna; Fernandez, Pablo Sebastian

Virulence on Pm4 kinase-based resistance is determined by two divergent wheat powdery mildew effectors

基于Pm4激酶的抗性毒力由两种不同的小麦白粉病效应因子决定。

Bernasconi, Zoe; Herger, Aline G; Caro, Maria Del Pilar; Kunz, Lukas; Müller, Marion C; Stirnemann, Ursin; Outram, Megan A; Widrig, Victoria; Neidhart, Matthias; Isaksson, Jonatan; Schudel, Seraina; Rösli, Sebastian; Wicker, Thomas; Bender, Kyle W; Zipfel, Cyril; Dodds, Peter N; Figueroa, Melania; Sánchez-Martín, Javier; Keller, Beat

Autocrine activity of engineered IL-33 mRNA enhances adoptive T-cell therapy for peritoneal carcinomatosis and synergizes with IL-12 mRNA.

工程化IL-33 mRNA的自分泌活性增强了过继性T细胞疗法对腹膜癌的疗效,并与IL-12 mRNA具有协同作用。

Arrizabalaga Leire, Di Trani Claudia Augusta, Gomar Celia, Moreno-Luqui Daniel, Ardaiz Nuria, Belsue Virginia, González-Gomariz José, Ruiz-Guillamon David, Risson Aline, Zheng Yufei, Huarte Eduardo, Matos Ignacio, Melero Ignacio, Berraondo Pedro, Aranda Fernando