Gene-Corrected Basal Cells Restore CFTR In Vitro; Transplants Regenerate Epithelium in a Preclinical Sinus Model
基因校正的基底细胞在体外恢复CFTR表达;移植可在临床前鼻窦模型中再生上皮
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doi:10.1101/2025.07.21.666023
Allan, Katelin M; Zhang, Shaoyan; Wong, Sharon L; Capraro, Alexander; McCarron, Alexandra; Skinner, Daniel; Kardia, Egi; Zheng, Ye; Zhong, Ling; Ng, Chai-Ann; Bell, Jessica L; Farrow, Nigel; Umashankar, Bala; Banks, Catherine; Herbert, Cristan; Kilian, Kristopher A; Pandzic, Elvis; Vittorio, Orazio; Vandenberg, Jamie I; Lock, John G; Jaffe, Adam; Donnelley, Martin; Parsons, David; Woodworth, Bradford A; Cho, Do-Yeon; Waters, Shafagh A