Adenovirus-associated virus vector-mediated gene transfer in hemophilia B
腺病毒相关病毒载体介导的B型血友病基因转移
期刊:New England Journal of Medicine
影响因子:78.5
doi:10.1056/NEJMoa1108046
Nathwani, Amit C; Tuddenham, Edward G D; Rangarajan, Savita; Rosales, Cecilia; McIntosh, Jenny; Linch, David C; Chowdary, Pratima; Riddell, Anne; Pie, Arnulfo Jaquilmac; Harrington, Chris; O'Beirne, James; Smith, Keith; Pasi, John; Glader, Bertil; Rustagi, Pradip; Ng, Catherine Y C; Kay, Mark A; Zhou, Junfang; Spence, Yunyu; Morton, Christopher L; Allay, James; Coleman, John; Sleep, Susan; Cunningham, John M; Srivastava, Deokumar; Basner-Tschakarjan, Etiena; Mingozzi, Federico; High, Katherine A; Gray, John T; Reiss, Ulrike M; Nienhuis, Arthur W; Davidoff, Andrew M