Integrated AAV optimization enables efficient gene delivery to kidney in murine and human tissue
整合的AAV优化技术可实现高效的基因递送至小鼠和人类肾脏组织。
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doi:10.21203/rs.3.rs-7925411/v1
Garcia, Fernando Gomez; Moreno, Miriam Rivera; Chetty, Shashank; Johnson, Najani; An, Andrea; Sostena, Juliet; Thompson, Lily; Wang, Jing; Charu, Vivek; Lee, Jean; Meyer, Natalie; Stoller, Marshall; Yang, Heiko; Boutagy, Nabil; DiRito, Jenna; Tietjen, Greg; Toscano, Catarina Allegue; Garcia-Gonzalez, Miguel; Church, George; Kay, Mark; Thakor, Avnesh; Bhalla, Vivek; Maxim, Demetrios