日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Pharmacological and pre-clinical safety profile of rSIV.F/HN, a hybrid lentiviral vector for cystic fibrosis gene therapy

rSIV.F/HN(一种用于囊性纤维化基因治疗的混合慢病毒载体)的药理学和临床前安全性概况

Moiseenko, Alena; Sinadinos, Anthony; Sergijenko, Ana; Pineault, Kyriel; Saleh, Aarash; Nekola, Konradin; Strang, Nathalie; Eleftheraki, Anastasia; Boyd, A Christopher; Davies, Jane C; Gill, Deborah R; Hyde, Stephen C; McLachlan, Gerry; Rath, Tim; Rothe, Michael; Schambach, Axel; Hobbie, Silke; Schuler, Michael; Maier, Udo; Thomas, Matthew J; Mennerich, Detlev; Schmidt, Manfred; Griesenbach, Uta; Alton, Eric W F W; Kreuz, Sebastian

Intranasal delivery of mRNA expressing newly identified Acinetobacter baumannii antigens protects against bacterial lung disease.

鼻内递送表达新发现的鲍曼不动杆菌抗原的mRNA可预防细菌性肺部疾病

Higham Sophie L, Wang Ziyin, Murugaiah Valarmathy, Song Jihye, Thomas Chubicka, Zhang Houze, Griesenbach Uta, Alton Eric W F W, Granger Luke A, Esparza Andrea Flores, Barbieri Beatriz Dias, Hitchen Paul G, Kellam Paul, Shattock Robin J, Sriskandan Shiranee, Reece Stephen T, Tregoning John S

Lentiviral Gene Therapy for Cystic Fibrosis: A Promising Approach and First-in-Human Trial

慢病毒基因疗法治疗囊性纤维化:一种前景广阔的方法和首次人体试验

Davies, Jane C; Polineni, Deepika; Boyd, A Christopher; Donaldson, Scott; Gill, Deborah R; Griesenbach, Uta; Hyde, Stephen C; Jain, Raksha; McLachlan, Gerry; Mall, Marcus A; Alton, Eric W F W

Lytic Bacteriophage Is a Promising Adjunct to Common Antibiotics across Cystic Fibrosis Clinical Strains and Culture Models of Pseudomonas aeruginosa Infection

溶菌噬菌体有望成为囊性纤维化临床菌株和铜绿假单胞菌感染培养模型中常用抗生素的辅助治疗手段

Martin, Isaac; Morales, Sandra; Alton, Eric W F W; Davies, Jane C

Progress in Respiratory Gene Therapy

呼吸系统基因治疗的进展

McLachlan, Gerry; Alton, Eric W F W; Boyd, A Christopher; Clarke, Nora K; Davies, Jane C; Gill, Deborah R; Griesenbach, Uta; Hickmott, Jack W; Hyde, Stephen C; Miah, Kamran M; Molina, Claudia Juarez

Identification and validation of a novel pathogenic variant in GDF2 (BMP9) responsible for hereditary hemorrhagic telangiectasia and pulmonary arteriovenous malformations.

鉴定和验证了 GDF2 (BMP9) 中一种新的致病变异,该变异导致遗传性出血性毛细血管扩张症和肺动静脉畸形

Balachandar Srimmitha, Graves Tamara J, Shimonty Anika, Kerr Katie, Kilner Jill, Xiao Sihao, Slade Richard, Sroya Manveer, Alikian Mary, Curetean Emanuel, Thomas Ellen, McConnell Vivienne P M, McKee Shane, Boardman-Pretty Freya, Devereau Andrew, Fowler Tom A, Caulfield Mark J, Alton Eric W, Ferguson Teena, Redhead Julian, McKnight Amy J, Thomas Geraldine A, Aldred Micheala A, Shovlin Claire L

Gene Therapy for Respiratory Diseases: Progress and a Changing Context

呼吸系统疾病基因治疗:进展与不断变化的环境

Alton, Eric W F W; Boyd, A Christopher; Davies, Jane C; Gill, Deborah R; Griesenbach, Uta; Harman, Tracy E; Hyde, Stephen; McLachlan, Gerry

The murine lung as a factory to produce secreted intrapulmonary and circulatory proteins

小鼠肺作为生产分泌型肺内蛋白和循环蛋白的工厂

Paul-Smith, Michael C; Pytel, Kamila M; Gelinas, Jean-François; McIntosh, Jenny; Pringle, Ian; Davies, Lee; Chan, Mario; Meng, Cuixiang; Bell, Robyn; Cammack, Lidia; Moran, Caroline; Cameron, Loren; Inoue, Makoto; Tsugumine, Shu; Hironaka, Takashi; Gill, Deborah R; Hyde, Stephen C; Nathwani, Amit; Alton, Eric W F W; Griesenbach, Uta

Preparation for a first-in-man lentivirus trial in patients with cystic fibrosis

为首次在囊性纤维化患者中开展慢病毒人体试验做准备

Alton, Eric W F W; Beekman, Jeffery M; Boyd, A Christopher; Brand, June; Carlon, Marianne S; Connolly, Mary M; Chan, Mario; Conlon, Sinead; Davidson, Heather E; Davies, Jane C; Davies, Lee A; Dekkers, Johanna F; Doherty, Ann; Gea-Sorli, Sabrina; Gill, Deborah R; Griesenbach, Uta; Hasegawa, Mamoru; Higgins, Tracy E; Hironaka, Takashi; Hyndman, Laura; McLachlan, Gerry; Inoue, Makoto; Hyde, Stephen C; Innes, J Alastair; Maher, Toby M; Moran, Caroline; Meng, Cuixiang; Paul-Smith, Michael C; Pringle, Ian A; Pytel, Kamila M; Rodriguez-Martinez, Andrea; Schmidt, Alexander C; Stevenson, Barbara J; Sumner-Jones, Stephanie G; Toshner, Richard; Tsugumine, Shu; Wasowicz, Marguerite W; Zhu, Jie

Antipseudomonal Bacteriophage Reduces Infective Burden and Inflammatory Response in Murine Lung

抗假单胞菌噬菌体可降低小鼠肺部的感染负荷和炎症反应

Pabary, Rishi; Singh, Charanjit; Morales, Sandra; Bush, Andrew; Alshafi, Khalid; Bilton, Diana; Alton, Eric W F W; Smithyman, Anthony; Davies, Jane C