Clinical Trial-Ready Patient Cohorts for Multiple System Atrophy: Coupling Biospecimen and iPSC Banking to Longitudinal Deep-Phenotyping
多系统萎缩的临床试验就绪患者队列:将生物样本和 iPSC 储存与纵向深度表型分析相结合
期刊:Cerebellum
影响因子:2.7
doi:10.1007/s12311-022-01471-8
Alain Ndayisaba, Ariana T Pitaro, Andrew S Willett, Kristie A Jones, Claudio Melo de Gusmao, Abby L Olsen, Jisoo Kim, Eero Rissanen, Jared K Woods, Sharan R Srinivasan, Anna Nagy, Amanda Nagy, Merlyne Mesidor, Steven Cicero, Viharkumar Patel, Derek H Oakley, Idil Tuncali, Katherine Taglieri-Noble, E