Paving the way toward treatment solutions for CTNNB1 syndrome: a patient organization perspective
为CTNNB1综合征的治疗方案铺平道路:患者组织的视角
期刊:Therapeutic Advances in Rare Disease
影响因子:
doi:10.1177/26330040251318355
Miroševič, Špela; Khandelwal, Shivang; Amerson, Emily; Parks, Effie; Parks, Mariana; Cochran, Lauren; González Hernández, Ana; Ferraro, Mirela; Lisowski, Leszek; Perez-Iturralde, Andrea; Chung, Wendy; Jacob, Michele H; Žakelj, Nina; Lainšček, Duško; Forstnerič, Vida; Sušjan, Petra; Maruna, Matea; Jerala, Roman; Osredkar, Damjan