日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

A prime editing strategy to rewrite the γ-globin promoters and reactivate fetal hemoglobin for sickle cell disease

镰状细胞病的主要编辑策略是重写γ-珠蛋白启动子并重新激活胎儿血红蛋白。

Chalumeau, Anne; Bou Dames, Maria; Fontana, Letizia; Amistadi, Simone; Antoniou, Panagiotis; Loganathan, Priyanka; Mombled, Margaux; Corre, Guillaume; Peterka, Martin; Amendola, Mario; Giovannangeli, Carine; Maresca, Marcello; Miccio, Annarita; Brusson, Mégane

Multiplex base editing of BCL11A regulatory elements to treat sickle cell disease

利用多重碱基编辑BCL11A调控元件治疗镰状细胞病

Letizia Fontana ,Pierre Martinucci ,Simone Amistadi ,Tristan Felix ,Margaux Mombled ,Alexandra Tachtsidi ,Guillaume Corre ,Anne Chalumeau ,Giulia Hardouin ,Jeanne Martin ,Oriana Romano ,Mario Amendola ,Panagiotis Antoniou ,Annarita Miccio

CoCas9 is a compact nuclease from the human microbiome for efficient and precise genome editing

CoCas9 是一种来自人类微生物组的紧凑型核酸酶,可实现高效、精确的基因组编辑

Eleonora Pedrazzoli #, Michele Demozzi #, Elisabetta Visentin #, Matteo Ciciani, Ilaria Bonuzzi, Laura Pezzè, Lorenzo Lucchetta, Giulia Maule, Simone Amistadi, Federica Esposito, Mariangela Lupo, Annarita Miccio, Alberto Auricchio, Antonio Casini, Nicola Segata, Anna Cereseto

Eukaryotic-driven directed evolution of Cas9 nucleases

真核生物驱动的Cas9核酸酶定向进化

Ruta, Giulia Vittoria; Ciciani, Matteo; Kheir, Eyemen; Gentile, Michele Domenico; Amistadi, Simone; Casini, Antonio; Cereseto, Anna

Functional restoration of a CFTR splicing mutation through RNA delivery of CRISPR adenine base editor

通过 RNA 递送 CRISPR 腺嘌呤碱基编辑器恢复 CFTR 剪接突变的功能

Simone Amistadi, Giulia Maule, Matteo Ciciani, Marjolein M Ensinck, Liesbeth De Keersmaecker, Anabela S Ramalho, Daniela Guidone, Martina Buccirossi, Luis J V Galietta, Marianne S Carlon, Anna Cereseto

An optimized SpCas9 high-fidelity variant for direct protein delivery

用于直接蛋白质递送的优化 SpCas9 高保真变体

Eleonora Pedrazzoli, Andrea Bianchi, Alessandro Umbach, Simone Amistadi, Mégane Brusson, Giacomo Frati, Matteo Ciciani, Kalina Aleksandra Badowska, Daniele Arosio, Annarita Miccio, Anna Cereseto, Antonio Casini

Resilient university campus in the city in COVID and post-COVID era—recommendations, guidelines, and evidence from research in Italy and Poland

在新冠疫情及后疫情时代,如何打造具有韧性的城市大学校园——来自意大利和波兰的研究建议、指南和证据

Luo, Shuang; Yi, Xinxin; Shao, Yiming; Xu, Jin; Amistadi, Lamberto; Bradecki, Tomasz; Uherek-Bradecka, Barbara

Removal of uranium from contaminated groundwater using monorhamnolipids and ion flotation

利用单鼠李糖脂和离子浮选法去除受污染地下水中的铀

Hogan, David E; Stolley, Ryan M; Boxley, Chett; Amistadi, Mary Kay; Maier, Raina M

Lung-Based, Exosome Inhibition Mediates Systemic Impacts Following Particulate Matter Exposure

肺外泌体抑制介导颗粒物暴露后的全身影响

Keegan Lopez, Alexandra Camacho, Quiteria Jacquez, Mary Kay Amistadi, Sebastian Medina, Katherine Zychowski

Differential Effects of Arsenic in Drinking Water on Mouse Hepatic and Intestinal Heme Oxygenase-1 Expression

饮用水中砷对小鼠肝脏和肠道血红素加氧酶-1表达的不同影响

Hui Li, Xiaoyu Fan, Xiangmeng Wu, Weiguo Han, Mary Kay Amistadi, Pengfei Liu, Donna Zhang, Jon Chorover, Xinxin Ding, Qing-Yu Zhang