Non-viral Gene Therapy for Stargardt Disease with ECO/pRHO-ABCA4 Self-Assembled Nanoparticles
利用ECO/pRHO-ABCA4自组装纳米颗粒进行非病毒基因治疗治疗Stargardt病
期刊:Molecular Therapy
影响因子:12.1
doi:10.1016/j.ymthe.2019.09.010
Da Sun ,Rebecca M Schur ,Avery E Sears ,Song-Qi Gao ,Amita Vaidya ,Wenyu Sun ,Akiko Maeda ,Timothy Kern ,Krzysztof Palczewski ,Zheng-Rong Lu