Indirect Comparison of Lenadogene Nolparvovec Gene Therapy Versus Natural History in Patients with Leber Hereditary Optic Neuropathy Carrying the m.11778G>A MT-ND4 Mutation
Lenadogene Nolparvovec基因治疗与自然病程在携带m.11778G>A MT-ND4突变的Leber遗传性视神经病变患者中的间接比较
期刊:Ophthalmology and Therapy
影响因子:3.2
doi:10.1007/s40123-022-00611-x
Carelli, Valerio; Newman, Nancy J; Yu-Wai-Man, Patrick; Biousse, Valerie; Moster, Mark L; Subramanian, Prem S; Vignal-Clermont, Catherine; Wang, An-Guor; Donahue, Sean P; Leroy, Bart P; Sergott, Robert C; Klopstock, Thomas; Sadun, Alfredo A; Rebolleda Fernández, Gema; Chwalisz, Bart K; Banik, Rudrani; Girmens, Jean François; La Morgia, Chiara; DeBusk, Adam A; Jurkute, Neringa; Priglinger, Claudia; Karanjia, Rustum; Josse, Constant; Salzmann, Julie; Montestruc, François; Roux, Michel; Taiel, Magali; Sahel, José-Alain