Allele-Specific Reduction of the Mutant Huntingtin Allele Using Transcription Activator-Like Effectors in Human Huntington's Disease Fibroblasts.
利用转录激活因子样效应物在人类亨廷顿病成纤维细胞中特异性降低突变亨廷顿等位基因
期刊:Cell Transplantation
影响因子:3.2
doi:10.3727/096368916X690863
Fink Kyle D, Deng Peter, Gutierrez Josh, Anderson Joseph S, Torrest Audrey, Komarla Anvita, Kalomoiris Stefanos, Cary Whitney, Anderson Johnathon D, Gruenloh William, Duffy Alexandra, Tempkin Teresa, Annett Geralyn, Wheelock Vicki, Segal David J, Nolta Jan A
