日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Intrathecal onasemnogene abeparvovec for treatment-experienced patients with spinal muscular atrophy: a phase 3b, open-label trial

鞘内注射onasemnogene abeparvovec治疗既往接受过治疗的脊髓性肌萎缩症患者:一项3b期开放标签试验

Kwon, Jennifer M; Munell, Francina; Le Goff, Laure; Yuge, Kotaro; Kato, Tamaki; Cances, Claude; De Waele, Liesbeth; Woodcock, Ian R; Mercuri, Eugenio M; Proud, Crystal M; Darras, Basil T; Hayes, Leslie H; Oskoui, Maryam; Visootsak, Jeannie; Williams, Gemma; Ilić, Andreja; Yang, Lina; van der Pol, W Ludo

Author Correction: Intrathecal onasemnogene abeparvovec for treatment-experienced patients with spinal muscular atrophy: a phase 3b, open-label trial

作者更正:鞘内注射onasemnogene abeparvovec治疗既往接受过治疗的脊髓性肌萎缩症患者:一项3b期开放标签试验

Kwon, Jennifer M; Munell, Francina; Le Goff, Laure; Yuge, Kotaro; Kato, Tamaki; Cances, Claude; De Waele, Liesbeth; Woodcock, Ian R; Mercuri, Eugenio M; Proud, Crystal M; Darras, Basil T; Hayes, Leslie H; Oskoui, Maryam; Visootsak, Jeannie; Williams, Gemma; Ilić, Andreja; Yang, Lina; van der Pol, W Ludo

Pyrimidinergic calcium signaling links tubular metabolism to fibrosis in kidney disease.

嘧啶能钙信号将肾小管代谢与肾脏疾病中的纤维化联系起来。

Figurek Andreja, Jankovic Nevena, Kollar Sarah, Kaminska Monika, Sakhi Imene, Rinaldi Anna, Cippà Pietro E, Robaye Bernard, Hall Andrew M

Reversible RNA ADP-ribosylation on uracil bases

尿嘧啶碱基上的可逆RNA ADP核糖基化

Lu, Yang; Tang, Li; Strømland, Øyvind; Chatrin, Chatrin; Zhu, Kang; Munnur, Deeksha; Groslambert, Joséphine; Mikolčević, Petra; Schüler, Herwig; Timinszky, Gyula; Gabant, Guillaume; Suskiewicz, Marcin J; Mikoč, Andreja; Aucagne, Vincent; Ahel, Dragana; Liu, Qiang; Ahel, Ivan

Safety and efficacy of intravenous onasemnogene abeparvovec gene therapy in patients with spinal muscular atrophy type 1: interim analysis from LT-001, a long-term follow-up study of patients from the START study

静脉注射onasemnogene abeparvovec基因疗法治疗1型脊髓性肌萎缩症患者的安全性和有效性:LT-001中期分析,一项对START研究患者进行的长期随访研究

Waldrop, Megan A; Escudero, Roberto Bernardo; Yang, Lina; Camarata, Rebekah A; Branic, Emily C; Mehl, Lesa; Ilić, Andreja; Connolly, Anne M

Cerebral Oximetry-Guided Treatment and Cerebral Oxygenation in Extremely Preterm Infants: A Randomized Clinical Trial

脑氧饱和度指导治疗和脑氧合在极早产儿中的应用:一项随机临床试验

Jani, Pranav R; Goyen, Traci-Anne; Balegar, Kiran Kumar; Maheshwari, Rajesh; Saito-Benz, Maria; Schindler, Tim; Moore, James; Merhi, Manelle; Cruz, Melinda; Song, Yang; McDonagh, Hayley; Luig, Melissa; Tracy, Mark; D'Cruz, Daphne; Perdomo, Aldo; Morakeas, Stephanie; Dasireddy, Vishnu; Culcer, Mihaela; Shingde, Vijay; Bennington, Karen; Michalowski, Joanna; Fucek, Andreja; Querim, Jennifer; Stevens, Sean; Santanelli, James; Elhindi, James; Gloss, Brian; Halliday, Robert; Shah, Dharmesh; Popat, Himanshu

KANK2 at focal adhesions regulates their maintenance and dynamics, while at fibrillar adhesions it influences cell migration via microtubule-dependent mechanism

KANK2 在黏着斑处调控其维持和动态变化,而在纤维状黏着斑处,它通过微管依赖性机制影响细胞迁移。

Stojanović, Nikolina; Rac, Anja; Lončarić, Marija; Tadijan, Ana; Paradžik, Mladen; Acman, Marta; Humphries, Jonathan D; Humphries, Martin J; Ambriović-Ristov, Andreja

miRNA expression profile as a potential tool for discrimination between bacterial and interstitial cystitis

miRNA表达谱作为区分细菌性膀胱炎和间质性膀胱炎的潜在工具

Peskar, Dominika; Kojc, Nika; Erman, Andreja; Boštjančič, Emanuela

Mechanistic Insights into AAV Capsid-Stationary Phase Interactions Governing Native Stability and Chromatographic Separation Using AAV8 as a Model System

以AAV8为模型系统,深入探究AAV衣壳-固定相相互作用对天然稳定性和色谱分离的影响机制

Žvanut, Timotej; Martelanc, Mitja; Štrancar, Aleš; Gramc Livk, Andreja

Truncated Equinin B Variants Reveal the Sequence Determinants of Antimicrobial Selectivity

截短的马来酸B变体揭示了抗菌选择性的序列决定因素

Staropoli, Mariele; Schwaiger, Theresa; Tuzlak, Jasmina; Biba, Renata; Petrowitsch, Lukas; Fessler, Johannes; Roje, Marin; Cammarata, Matteo; Malanović, Nermina; Jakas, Andreja