Translation from a DMD exon 5 IRES results in a functional dystrophin isoform that attenuates dystrophinopathy in humans and mice
DMD 外显子 5 IRES 的翻译可产生功能性肌营养不良蛋白异构体，从而减轻人类和小鼠的肌营养不良蛋白病
期刊:Nature Medicine
影响因子:58.7
doi:10.1038/nm.3628
Nicolas Wein, Adeline Vulin, Maria S Falzarano, Christina Al-Khalili Szigyarto, Baijayanta Maiti, Andrew Findlay, Kristin N Heller, Mathias Uhlén, Baskar Bakthavachalu, Sonia Messina, Giuseppe Vita, Chiara Passarelli, Simona Brioschi, Matteo Bovolenta, Marcella Neri, Francesca Gualandi, Steve D Wilt
